Showing results (141-150 of 152) with videos related to
Sort By:
Pageof 16
Molecular Therapy. Methods & Clinical Development|March 6, 2023
Micro-dystrophin gene therapy demonstrates long-term cardiac efficacy in a severe Duchenne muscular dystrophy modelArden B Piepho, Jeovanna Lowe, Laurel R Cumby, et al.Human Molecular Genetics|August 2, 2014
Phosphorylation within the cysteine-rich region of dystrophin enhances its association with β-dystroglycan and identifies a potential novel therapeutic target for skeletal muscle wastingKristy Swiderski, Scott A Shaffer, Byron Gallis, et al.JCI Insight|May 1, 2019
Stabilization of the cardiac sarcolemma by sarcospan rescues DMD-associated cardiomyopathyMichelle S Parvatiyar, Alexandra J Brownstein, Rosemeire M Kanashiro-Takeuchi, et al.The Journal of Cell Biology|June 20, 2012
Follistatin-mediated skeletal muscle hypertrophy is regulated by Smad3 and mTOR independently of myostatinCatherine E Winbanks, Kate L Weeks, Rachel E Thomson, et al.Nature Cell Biology|February 13, 2007
Pericytes of human skeletal muscle are myogenic precursors distinct from satellite cellsArianna Dellavalle, Maurilio Sampaolesi, Rossana Tonlorenzi, et al.The Journal of Clinical Investigation|September 18, 2002
Long-term persistence of donor nuclei in a Duchenne muscular dystrophy patient receiving bone marrow transplantationEmanuela Gussoni, Richard R Bennett, Kristina R Muskiewicz, et al.Proceedings of the National Academy of Sciences of the United States of America|November 8, 2023
In vivo selection of synthetic nucleocapsids for tissue targetingAudrey Olshefsky, Halli Benasutti, Meilyn Sylvestre, et al.Nature Communications|October 2, 2019
High levels of AAV vector integration into CRISPR-induced DNA breaksKillian S Hanlon, Benjamin P Kleinstiver, Sara P Garcia, et al.Human Gene Therapy|February 6, 2015
Perspectives on best practices for gene therapy programsThomas R Cheever, Dale Berkley, Serge Braun, et al.Nature Metabolism|March 21, 2023
PCYT2-regulated lipid biosynthesis is critical to muscle health and ageingDomagoj Cikes, Kareem Elsayad, Erdinc Sezgin, et al.Pageof 16