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Brain : a Journal of Neurology
|
June 4, 2009
Exhaustive analysis of BH4 and dopamine biosynthesis genes in patients with Dopa-responsive dystonia
Fabienne Clot, David Grabli, Cécile Cazeneuve, et al.
European Journal of Human Genetics : EJHG
|
December 16, 2018
A National French consensus on gene lists for the diagnosis of myopathies using next-generation sequencing
Martin Krahn, Valérie Biancalana, Mathieu Cerino, et al.
Frontiers in Pediatrics
|
March 6, 2020
Palliative Care in SMA Type 1: A Prospective Multicenter French Study Based on Parents' Reports
Marie Hully, Christine Barnerias, Delphine Chabalier, et al.
Acta Neuropathologica
|
January 15, 2013
VMA21 deficiency prevents vacuolar ATPase assembly and causes autophagic vacuolar myopathy
Nivetha Ramachandran, Iulia Munteanu, Peixiang Wang, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
March 17, 2009
Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease
Marc Nicolino, Barry Byrne, J Edmund Wraith, et al.
Journal of Inherited Metabolic Disease
|
March 22, 2017
Neurocognitive profiles in MSUD school-age patients
Juliette Bouchereau, Julie Leduc-Leballeur, Samia Pichard, et al.
Cell
|
April 22, 2009
VMA21 deficiency causes an autophagic myopathy by compromising V-ATPase activity and lysosomal acidification
Nivetha Ramachandran, Iulia Munteanu, Peixiang Wang, et al.
The Journal of Pediatrics
|
October 20, 2022
Individual and Family Determinants for Quality of Life in Parents of Children with Inborn Errors of Metabolism Requiring a Restricted Diet: A Multilevel Analysis Approach
Abdoulaye Ouattara, Noemie Resseguier, Aline Cano, et al.
Journal of Clinical Medicine
|
July 26, 2020
A Cross-Sectional Retrospective Study of Non-Splenectomized and Never-Treated Patients with Type 1 Gaucher Disease
Christine Serratrice, Jérôme Stirnemann, Amina Berrahal, et al.
The Journal of Pediatrics
|
March 9, 2020
Health Status of French Young Patients with Inborn Errors of Metabolism with Lifelong Restricted Diet
Aline Cano, Noemie Resseguier, Abdoulaye Ouattara, et al.
Page
of 15
Search research articles
Search
Showing results (101-110 of 147) with videos related to
Sort By:
Page
of 15
Brain : a Journal of Neurology
|
June 4, 2009
Exhaustive analysis of BH4 and dopamine biosynthesis genes in patients with Dopa-responsive dystonia
Fabienne Clot, David Grabli, Cécile Cazeneuve, et al.
European Journal of Human Genetics : EJHG
|
December 16, 2018
A National French consensus on gene lists for the diagnosis of myopathies using next-generation sequencing
Martin Krahn, Valérie Biancalana, Mathieu Cerino, et al.
Frontiers in Pediatrics
|
March 6, 2020
Palliative Care in SMA Type 1: A Prospective Multicenter French Study Based on Parents' Reports
Marie Hully, Christine Barnerias, Delphine Chabalier, et al.
Acta Neuropathologica
|
January 15, 2013
VMA21 deficiency prevents vacuolar ATPase assembly and causes autophagic vacuolar myopathy
Nivetha Ramachandran, Iulia Munteanu, Peixiang Wang, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
March 17, 2009
Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease
Marc Nicolino, Barry Byrne, J Edmund Wraith, et al.
Journal of Inherited Metabolic Disease
|
March 22, 2017
Neurocognitive profiles in MSUD school-age patients
Juliette Bouchereau, Julie Leduc-Leballeur, Samia Pichard, et al.
Cell
|
April 22, 2009
VMA21 deficiency causes an autophagic myopathy by compromising V-ATPase activity and lysosomal acidification
Nivetha Ramachandran, Iulia Munteanu, Peixiang Wang, et al.
The Journal of Pediatrics
|
October 20, 2022
Individual and Family Determinants for Quality of Life in Parents of Children with Inborn Errors of Metabolism Requiring a Restricted Diet: A Multilevel Analysis Approach
Abdoulaye Ouattara, Noemie Resseguier, Aline Cano, et al.
Journal of Clinical Medicine
|
July 26, 2020
A Cross-Sectional Retrospective Study of Non-Splenectomized and Never-Treated Patients with Type 1 Gaucher Disease
Christine Serratrice, Jérôme Stirnemann, Amina Berrahal, et al.
The Journal of Pediatrics
|
March 9, 2020
Health Status of French Young Patients with Inborn Errors of Metabolism with Lifelong Restricted Diet
Aline Cano, Noemie Resseguier, Abdoulaye Ouattara, et al.
Page
of 15