Search research articles
Contact Us
Filters
Showing results (131-140 of 147) with videos related to
Page
of 15
Sort By:
Journal of Medical Genetics
|
July 13, 2013
Prevalence of rare mitochondrial DNA mutations in mitochondrial disorders
Sylvie Bannwarth, Vincent Procaccio, Anne Sophie Lebre, et al.
Journal of Medical Genetics
|
March 19, 2021
Disentangling molecular and clinical stratification patterns in beta-galactosidase deficiency
Abdellah Tebani, Bénédicte Sudrié-Arnaud, Ivana Dabaj, et al.
European Heart Journal
|
March 22, 2021
Association between prophylactic angiotensin-converting enzyme inhibitors and overall survival in Duchenne muscular dystrophy-analysis of registry data
Raphaël Porcher, Isabelle Desguerre, Helge Amthor, et al.
Journal of Medical Genetics
|
September 29, 2017
Clinical, laboratory and molecular findings and long-term follow-up data in 96 French patients with PMM2-CDG (phosphomannomutase 2-congenital disorder of glycosylation) and review of the literature
Manuel Schiff, Céline Roda, Marie-Lorraine Monin, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
November 4, 2022
Expanding SPTAN1 monoallelic variant associated disorders: From epileptic encephalopathy to pure spastic paraplegia and ataxia
Heba Morsy, Mehdi Benkirane, Elisa Cali, et al.
BMJ Open
|
October 23, 2025
PERIGENOMED-CLINICS 1-the first study on feasibility, acceptability and psychosocial impact of PERIGENOMED: a pilot project aimed at providing initial concrete evidence on the relevance of panel-based genome sequencing for newborn screening (NBS) in France
Camille Level, Christel Thauvin-Robinet, Christine Binquet, et al.
Orphanet Journal of Rare Diseases
|
October 17, 2015
Expanding the clinical spectrum of hereditary fibrosing poikiloderma with tendon contractures, myopathy and pulmonary fibrosis due to FAM111B mutations
Sandra Mercier, Sébastien Küry, Emmanuelle Salort-Campana, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 10, 2021
Biallelic variants in PCDHGC4 cause a novel neurodevelopmental syndrome with progressive microcephaly, seizures, and joint anomalies
Maria Iqbal, Reza Maroofian, Büşranur Çavdarlı, et al.
Journal of Inherited Metabolic Disease
|
June 17, 2015
Erratum to: The phenotypic spectrum of organic acidurias and urea cycle disorders. Part 1: the initial presentation
Stefan Kölker, Angeles Garcia Cazorla, Vassili Valayannopoulos, et al.
Brain : a Journal of Neurology
|
February 5, 2010
Glucose transporter-1 deficiency syndrome: the expanding clinical and genetic spectrum of a treatable disorder
Wilhelmina G Leen, Joerg Klepper, Marcel M Verbeek, et al.
Page
of 15
Search research articles
Search
Showing results (131-140 of 147) with videos related to
Sort By:
Page
of 15
Journal of Medical Genetics
|
July 13, 2013
Prevalence of rare mitochondrial DNA mutations in mitochondrial disorders
Sylvie Bannwarth, Vincent Procaccio, Anne Sophie Lebre, et al.
Journal of Medical Genetics
|
March 19, 2021
Disentangling molecular and clinical stratification patterns in beta-galactosidase deficiency
Abdellah Tebani, Bénédicte Sudrié-Arnaud, Ivana Dabaj, et al.
European Heart Journal
|
March 22, 2021
Association between prophylactic angiotensin-converting enzyme inhibitors and overall survival in Duchenne muscular dystrophy-analysis of registry data
Raphaël Porcher, Isabelle Desguerre, Helge Amthor, et al.
Journal of Medical Genetics
|
September 29, 2017
Clinical, laboratory and molecular findings and long-term follow-up data in 96 French patients with PMM2-CDG (phosphomannomutase 2-congenital disorder of glycosylation) and review of the literature
Manuel Schiff, Céline Roda, Marie-Lorraine Monin, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
November 4, 2022
Expanding SPTAN1 monoallelic variant associated disorders: From epileptic encephalopathy to pure spastic paraplegia and ataxia
Heba Morsy, Mehdi Benkirane, Elisa Cali, et al.
BMJ Open
|
October 23, 2025
PERIGENOMED-CLINICS 1-the first study on feasibility, acceptability and psychosocial impact of PERIGENOMED: a pilot project aimed at providing initial concrete evidence on the relevance of panel-based genome sequencing for newborn screening (NBS) in France
Camille Level, Christel Thauvin-Robinet, Christine Binquet, et al.
Orphanet Journal of Rare Diseases
|
October 17, 2015
Expanding the clinical spectrum of hereditary fibrosing poikiloderma with tendon contractures, myopathy and pulmonary fibrosis due to FAM111B mutations
Sandra Mercier, Sébastien Küry, Emmanuelle Salort-Campana, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 10, 2021
Biallelic variants in PCDHGC4 cause a novel neurodevelopmental syndrome with progressive microcephaly, seizures, and joint anomalies
Maria Iqbal, Reza Maroofian, Büşranur Çavdarlı, et al.
Journal of Inherited Metabolic Disease
|
June 17, 2015
Erratum to: The phenotypic spectrum of organic acidurias and urea cycle disorders. Part 1: the initial presentation
Stefan Kölker, Angeles Garcia Cazorla, Vassili Valayannopoulos, et al.
Brain : a Journal of Neurology
|
February 5, 2010
Glucose transporter-1 deficiency syndrome: the expanding clinical and genetic spectrum of a treatable disorder
Wilhelmina G Leen, Joerg Klepper, Marcel M Verbeek, et al.
Page
of 15