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March 24, 2012
Molecular analysis of HEXA gene in Argentinean patients affected with Tay-Sachs disease: possible common origin of the prevalent c.459+5A>G mutation
Stefania Zampieri, Annalisa Montalvo, Mariana Blanco, et al.
Human Mutation
|
December 18, 2004
Identification and functional characterization of five novel mutant alleles in 58 Italian patients with Gaucher disease type 1
Snjezana Miocić, Mirella Filocamo, Silvia Dominissini, et al.
Value in Health : the Journal of the International Society for Pharmacoeconomics and Outcomes Research
|
September 13, 2019
Value of the Rare Disease Registry of the Italian Region Friuli Venezia Giulia
Francesca Valent, Laura Deroma, Alessandro Moro, et al.
Human Mutation
|
February 16, 2005
Identification and characterization of five novel MAN2B1 mutations in Italian patients with alpha-mannosidosis
Michele Sbaragli, Lucia Bibi, Maria Gabriela Pittis, et al.
Rice (New York, N.Y.)
|
November 28, 2013
Endosperm-specific expression of human acid beta-glucosidase in a waxy rice
Tamara Patti, Bruno Bembi, Piero Cristin, et al.
Molecular Genetics and Metabolism Reports
|
December 9, 2020
<i>In vitro</i> and <i>in vivo</i> effects of Ambroxol chaperone therapy in two Italian patients affected by neuronopathic Gaucher disease and epilepsy
Giovanni Ciana, Andrea Dardis, Eleonora Pavan, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
March 24, 2010
The angiotensin-converting enzyme insertion/deletion polymorphism modifies the clinical outcome in patients with Pompe disease
Paola de Filippi, Sabrina Ravaglia, Bruno Bembi, et al.
Journal of Neuromuscular Diseases
|
November 19, 2016
Changing Characteristics of Late-Onset Pompe Disease Patients in Italy: Data from the Pompe Registry
Corrado Angelini, Bruno Bembi, Alberto Burlina, et al.
Orphanet Journal of Rare Diseases
|
September 18, 2014
Effects of miglustat treatment in a patient affected by an atypical form of Tangier disease
Annalisa Sechi, Andrea Dardis, Stefania Zampieri, et al.
Journal of Inherited Metabolic Disease
|
November 17, 2017
Newborn screening for lysosomal storage disorders by tandem mass spectrometry in North East Italy
Alberto B Burlina, Giulia Polo, Leonardo Salviati, et al.
Page
of 11
Search research articles
Search
Showing results (51-60 of 101) with videos related to
Sort By:
Page
of 11
Gene
|
March 24, 2012
Molecular analysis of HEXA gene in Argentinean patients affected with Tay-Sachs disease: possible common origin of the prevalent c.459+5A>G mutation
Stefania Zampieri, Annalisa Montalvo, Mariana Blanco, et al.
Human Mutation
|
December 18, 2004
Identification and functional characterization of five novel mutant alleles in 58 Italian patients with Gaucher disease type 1
Snjezana Miocić, Mirella Filocamo, Silvia Dominissini, et al.
Value in Health : the Journal of the International Society for Pharmacoeconomics and Outcomes Research
|
September 13, 2019
Value of the Rare Disease Registry of the Italian Region Friuli Venezia Giulia
Francesca Valent, Laura Deroma, Alessandro Moro, et al.
Human Mutation
|
February 16, 2005
Identification and characterization of five novel MAN2B1 mutations in Italian patients with alpha-mannosidosis
Michele Sbaragli, Lucia Bibi, Maria Gabriela Pittis, et al.
Rice (New York, N.Y.)
|
November 28, 2013
Endosperm-specific expression of human acid beta-glucosidase in a waxy rice
Tamara Patti, Bruno Bembi, Piero Cristin, et al.
Molecular Genetics and Metabolism Reports
|
December 9, 2020
<i>In vitro</i> and <i>in vivo</i> effects of Ambroxol chaperone therapy in two Italian patients affected by neuronopathic Gaucher disease and epilepsy
Giovanni Ciana, Andrea Dardis, Eleonora Pavan, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
March 24, 2010
The angiotensin-converting enzyme insertion/deletion polymorphism modifies the clinical outcome in patients with Pompe disease
Paola de Filippi, Sabrina Ravaglia, Bruno Bembi, et al.
Journal of Neuromuscular Diseases
|
November 19, 2016
Changing Characteristics of Late-Onset Pompe Disease Patients in Italy: Data from the Pompe Registry
Corrado Angelini, Bruno Bembi, Alberto Burlina, et al.
Orphanet Journal of Rare Diseases
|
September 18, 2014
Effects of miglustat treatment in a patient affected by an atypical form of Tangier disease
Annalisa Sechi, Andrea Dardis, Stefania Zampieri, et al.
Journal of Inherited Metabolic Disease
|
November 17, 2017
Newborn screening for lysosomal storage disorders by tandem mass spectrometry in North East Italy
Alberto B Burlina, Giulia Polo, Leonardo Salviati, et al.
Page
of 11