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Science Translational Medicine
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January 27, 2017
Tau reduction prevents neuronal loss and reverses pathological tau deposition and seeding in mice with tauopathy
Sarah L DeVos, Rebecca L Miller, Kathleen M Schoch, et al.
Neurology
|
April 26, 2019
Nusinersen in later-onset spinal muscular atrophy: Long-term results from the phase 1/2 studies
Basil T Darras, Claudia A Chiriboga, Susan T Iannaccone, et al.
Nature Communications
|
August 11, 2015
DNA/RNA heteroduplex oligonucleotide for highly efficient gene silencing
Kazutaka Nishina, Wenying Piao, Kie Yoshida-Tanaka, et al.
American Journal of Human Genetics
|
August 9, 2016
The Power of Human Protective Modifiers: PLS3 and CORO1C Unravel Impaired Endocytosis in Spinal Muscular Atrophy and Rescue SMA Phenotype
Seyyedmohsen Hosseinibarkooie, Miriam Peters, Laura Torres-Benito, et al.
Nature Neuroscience
|
January 16, 2019
Premature polyadenylation-mediated loss of stathmin-2 is a hallmark of TDP-43-dependent neurodegeneration
Ze'ev Melamed, Jone López-Erauskin, Michael W Baughn, et al.
The Lancet. Neurology
|
April 2, 2013
An antisense oligonucleotide against SOD1 delivered intrathecally for patients with SOD1 familial amyotrophic lateral sclerosis: a phase 1, randomised, first-in-man study
Timothy M Miller, Alan Pestronk, William David, et al.
Nucleic Acids Research
|
November 11, 2015
Hepatotoxicity of high affinity gapmer antisense oligonucleotides is mediated by RNase H1 dependent promiscuous reduction of very long pre-mRNA transcripts
Sebastien A Burel, Christopher E Hart, Patrick Cauntay, et al.
Science Translational Medicine
|
October 25, 2013
Targeting RNA foci in iPSC-derived motor neurons from ALS patients with a C9ORF72 repeat expansion
Dhruv Sareen, Jacqueline G O'Rourke, Pratap Meera, et al.
Journal of Medicinal Chemistry
|
April 16, 2004
Structure-activity relationship of purine ribonucleosides for inhibition of hepatitis C virus RNA-dependent RNA polymerase
Anne B Eldrup, Charles R Allerson, C Frank Bennett, et al.
Nature Biotechnology
|
August 13, 2021
Cholesterol-functionalized DNA/RNA heteroduplexes cross the blood-brain barrier and knock down genes in the rodent CNS
Tetsuya Nagata, Chrissa A Dwyer, Kie Yoshida-Tanaka, et al.
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of 17
Search research articles
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Showing results (131-140 of 169) with videos related to
Sort By:
Page
of 17
Science Translational Medicine
|
January 27, 2017
Tau reduction prevents neuronal loss and reverses pathological tau deposition and seeding in mice with tauopathy
Sarah L DeVos, Rebecca L Miller, Kathleen M Schoch, et al.
Neurology
|
April 26, 2019
Nusinersen in later-onset spinal muscular atrophy: Long-term results from the phase 1/2 studies
Basil T Darras, Claudia A Chiriboga, Susan T Iannaccone, et al.
Nature Communications
|
August 11, 2015
DNA/RNA heteroduplex oligonucleotide for highly efficient gene silencing
Kazutaka Nishina, Wenying Piao, Kie Yoshida-Tanaka, et al.
American Journal of Human Genetics
|
August 9, 2016
The Power of Human Protective Modifiers: PLS3 and CORO1C Unravel Impaired Endocytosis in Spinal Muscular Atrophy and Rescue SMA Phenotype
Seyyedmohsen Hosseinibarkooie, Miriam Peters, Laura Torres-Benito, et al.
Nature Neuroscience
|
January 16, 2019
Premature polyadenylation-mediated loss of stathmin-2 is a hallmark of TDP-43-dependent neurodegeneration
Ze'ev Melamed, Jone López-Erauskin, Michael W Baughn, et al.
The Lancet. Neurology
|
April 2, 2013
An antisense oligonucleotide against SOD1 delivered intrathecally for patients with SOD1 familial amyotrophic lateral sclerosis: a phase 1, randomised, first-in-man study
Timothy M Miller, Alan Pestronk, William David, et al.
Nucleic Acids Research
|
November 11, 2015
Hepatotoxicity of high affinity gapmer antisense oligonucleotides is mediated by RNase H1 dependent promiscuous reduction of very long pre-mRNA transcripts
Sebastien A Burel, Christopher E Hart, Patrick Cauntay, et al.
Science Translational Medicine
|
October 25, 2013
Targeting RNA foci in iPSC-derived motor neurons from ALS patients with a C9ORF72 repeat expansion
Dhruv Sareen, Jacqueline G O'Rourke, Pratap Meera, et al.
Journal of Medicinal Chemistry
|
April 16, 2004
Structure-activity relationship of purine ribonucleosides for inhibition of hepatitis C virus RNA-dependent RNA polymerase
Anne B Eldrup, Charles R Allerson, C Frank Bennett, et al.
Nature Biotechnology
|
August 13, 2021
Cholesterol-functionalized DNA/RNA heteroduplexes cross the blood-brain barrier and knock down genes in the rodent CNS
Tetsuya Nagata, Chrissa A Dwyer, Kie Yoshida-Tanaka, et al.
Page
of 17