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Brain : a Journal of Neurology|January 29, 2024
Viral-based animal models in polyglutamine disordersCarina Henriques, Miguel M Lopes, Ana C Silva, et al.
Experimental Neurology|August 3, 2025
Differential impact of mutant Ataxin-3 in hindbrain regions: further evidence of white matter loss as a core pathological featureCarina Henriques, Marta Silva, António Silva, et al.
Molecular Therapy. Methods & Clinical Development|September 11, 2020
Simple and Fast SEC-Based Protocol to Isolate Human Plasma-Derived Extracellular Vesicles for Transcriptional ResearchLaetitia S Gaspar, Magda M Santana, Carina Henriques, et al.
Journal of Visualized Experiments : Jove|April 22, 2024
Isolation of Adeno-associated Viral Vectors Through a Single-step and Semi-automated Heparin Affinity Chromatography ProtocolMiguel M Lopes, Sara M Lopes, Rafael Baganha, et al.
Brain : a Journal of Neurology|November 19, 2019
Antisense oligonucleotide therapeutics in neurodegenerative diseases: the case of polyglutamine disordersAna C Silva, Diana D Lobo, Inês M Martins, et al.
Cell Death & Disease|November 30, 2021
Autophagy in Spinocerebellar ataxia type 2, a dysregulated pathway, and a target for therapyAdriana Marcelo, Inês T Afonso, Ricardo Afonso-Reis, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|April 7, 2023
Extracellular vesicle-based delivery of silencing sequences for the treatment of Machado-Joseph disease/spinocerebellar ataxia type 3David Rufino-Ramos, Patrícia R Albuquerque, Kevin Leandro, et al.
Nucleic Acid Therapeutics|December 8, 2021
miRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3Rui Jorge Nobre, Diana D Lobo, Carina Henriques, et al.
Biomaterials|March 14, 2026
Extracellular vesicles-mediated delivery of SpCas9 RNPs for therapeutic gene editing in Spinocerebellar Ataxia Type 3Kevin Leandro, David Rufino-Ramos, Sara M Lopes, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|October 13, 2025
Extracellular vesicles-associated AAVs for the treatment of Machado-Joseph diseaseCarina Henriques, Patrícia Albuquerque, David Rufino-Ramos, et al.
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