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Showing results (61-70 of 83) with videos related to
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Muscle & Nerve
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February 18, 2022
Cardiac and pulmonary findings in dysferlinopathy: A 3-year, longitudinal study
Ursula Moore, Roberto Fernandez-Torron, Marni Jacobs, et al.
Brain : a Journal of Neurology
|
July 24, 2024
Decoding the muscle transcriptome of patients with late-onset Pompe disease reveals markers of disease progression
Alexandra Monceau, Rasya Gokul Nath, Xavier Suárez-Calvet, et al.
Neurology
|
February 20, 2020
Clinical and therapeutic features of myasthenia gravis in adults based on age at onset
Elena Cortés-Vicente, Rodrigo Álvarez-Velasco, Sonia Segovia, et al.
European Journal of Neurology
|
March 15, 2021
Clinical characteristics and outcomes of thymoma-associated myasthenia gravis
Rodrigo Álvarez-Velasco, Gerardo Gutiérrez-Gutiérrez, Juan Carlos Trujillo, et al.
Brain : a Journal of Neurology
|
March 13, 2023
Anoctamin-5 related muscle disease: clinical and genetic findings in a large European cohort
Alexander de Bruyn, Federica Montagnese, Sonja Holm-Yildiz, et al.
Neurology. Genetics
|
September 8, 2016
The Clinical Outcome Study for dysferlinopathy: An international multicenter study
Elizabeth Harris, Catherine L Bladen, Anna Mayhew, et al.
Orphanet Journal of Rare Diseases
|
February 14, 2024
EURO-NMD registry: federated FAIR infrastructure, innovative technologies and concepts of a patient-centred registry for rare neuromuscular disorders
Antonio Atalaia, Dagmar Wandrei, Nawel Lalout, et al.
Journal of Neurology, Neurosurgery, and Psychiatry
|
January 31, 2018
Teenage exercise is associated with earlier symptom onset in dysferlinopathy: a retrospective cohort study
Ursula R Moore, Marni Jacobs, Roberto Fernandez-Torron, et al.
Brain : a Journal of Neurology
|
November 12, 2024
HMGCS1 variants cause rigid spine syndrome amenable to mevalonic acid treatment in an animal model
Lein N H Dofash, Lee B Miles, Yoshihiko Saito, et al.
Journal of Neuromuscular Diseases
|
July 29, 2025
Real-world data on spinal muscular atrophy in Spain: Insights from over 500 individuals in the CuidAME project
Cristina Puig-Ram, Sonia Segovia, Rocio Garcia-Uzquiano, et al.
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of 9
Search research articles
Search
Showing results (61-70 of 83) with videos related to
Sort By:
Page
of 9
Muscle & Nerve
|
February 18, 2022
Cardiac and pulmonary findings in dysferlinopathy: A 3-year, longitudinal study
Ursula Moore, Roberto Fernandez-Torron, Marni Jacobs, et al.
Brain : a Journal of Neurology
|
July 24, 2024
Decoding the muscle transcriptome of patients with late-onset Pompe disease reveals markers of disease progression
Alexandra Monceau, Rasya Gokul Nath, Xavier Suárez-Calvet, et al.
Neurology
|
February 20, 2020
Clinical and therapeutic features of myasthenia gravis in adults based on age at onset
Elena Cortés-Vicente, Rodrigo Álvarez-Velasco, Sonia Segovia, et al.
European Journal of Neurology
|
March 15, 2021
Clinical characteristics and outcomes of thymoma-associated myasthenia gravis
Rodrigo Álvarez-Velasco, Gerardo Gutiérrez-Gutiérrez, Juan Carlos Trujillo, et al.
Brain : a Journal of Neurology
|
March 13, 2023
Anoctamin-5 related muscle disease: clinical and genetic findings in a large European cohort
Alexander de Bruyn, Federica Montagnese, Sonja Holm-Yildiz, et al.
Neurology. Genetics
|
September 8, 2016
The Clinical Outcome Study for dysferlinopathy: An international multicenter study
Elizabeth Harris, Catherine L Bladen, Anna Mayhew, et al.
Orphanet Journal of Rare Diseases
|
February 14, 2024
EURO-NMD registry: federated FAIR infrastructure, innovative technologies and concepts of a patient-centred registry for rare neuromuscular disorders
Antonio Atalaia, Dagmar Wandrei, Nawel Lalout, et al.
Journal of Neurology, Neurosurgery, and Psychiatry
|
January 31, 2018
Teenage exercise is associated with earlier symptom onset in dysferlinopathy: a retrospective cohort study
Ursula R Moore, Marni Jacobs, Roberto Fernandez-Torron, et al.
Brain : a Journal of Neurology
|
November 12, 2024
HMGCS1 variants cause rigid spine syndrome amenable to mevalonic acid treatment in an animal model
Lein N H Dofash, Lee B Miles, Yoshihiko Saito, et al.
Journal of Neuromuscular Diseases
|
July 29, 2025
Real-world data on spinal muscular atrophy in Spain: Insights from over 500 individuals in the CuidAME project
Cristina Puig-Ram, Sonia Segovia, Rocio Garcia-Uzquiano, et al.
Page
of 9