Showing results (21-30 of 29) with videos related to

Sort By:
Pageof 3
You have reached the last page of results.This site can display upto 29 results.
Haemophilia : the Official Journal of the World Federation of Hemophilia|January 27, 2025
Operationalising a Haemophilia Gene Editing Lexicon for Practical UseWilliam McKeown, Cedric Hermans, Carmen Unzu, et al.
Nature Communications|March 16, 2022
Choice of vector and surgical approach enables efficient cochlear gene transfer in nonhuman primateEva Andres-Mateos, Lukas D Landegger, Carmen Unzu, et al.
Haemophilia : the Official Journal of the World Federation of Hemophilia|October 22, 2024
A novel gene editing lexicon strategy for the haemophilia community: Research plan for development and preliminary resultsCedric Hermans, Leonard A Valentino, Courtney D Thornburg, et al.
Cell Reports. Medicine|November 3, 2022
Ancestral library identifies conserved reprogrammable liver motif on AAV capsidEric Zinn, Carmen Unzu, Pauline F Schmit, et al.
Research and Practice in Thrombosis and Haemostasis|April 16, 2025
Development of a novel gene editing lexicon for hemophilia: methodology and resultsCraig M Kessler, Leonard A Valentino, Courtney D Thornburg, et al.
Nature Communications|March 15, 2024
Harnessing whole human liver ex situ normothermic perfusion for preclinical AAV vector evaluationMarti Cabanes-Creus, Sophia H Y Liao, Renina Gale Navarro, et al.
Human Gene Therapy|September 28, 2013
Safety and liver transduction efficacy of rAAV5-cohPBGD in nonhuman primates: a potential therapy for acute intermittent porphyriaAstrid Pañeda, Esperanza Lopez-Franco, Christine Kaeppel, et al.
Cancer Cell|March 24, 2026
Radiotherapy synergizes with an inducible AAV-based immunotherapy platform to program local and systemic antitumor immunitySonia Marco, Myriam Fernández, Beatriz Honorato, et al.
Gut|October 4, 2024
Systemic messenger RNA replacement therapy is effective in a novel clinically relevant model of acute intermittent porphyria developed in non-human primatesKarol M Córdoba, Daniel Jericó, Lei Jiang, et al.
Pageof 3