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Neurobiology of Disease
|
December 17, 2009
Induced secretion of beta-hexosaminidase by human brain endothelial cells: a novel approach in Sandhoff disease?
Lionel Batista, Florence Miller, Céline Clave, et al.
Orphanet Journal of Rare Diseases
|
July 2, 2014
Modeling changes in biomarkers in Gaucher disease patients receiving enzyme replacement therapy using a pathophysiological model
Marie Vigan, Jérôme Stirnemann, Catherine Caillaud, et al.
American Journal of Medical Genetics. Part A
|
November 18, 2008
Developmental delay, dysmorphic features, neonatal spontaneous fractures, wrinkled skin, and hepatic failure: a new metabolic syndrome?
André Mégarbané, Leila Samaras, Rima Chédid, et al.
Neuromuscular Disorders : NMD
|
December 17, 2009
Rigid spine syndrome revealing late-onset Pompe disease
Pascal Laforêt, Valérie Doppler, Catherine Caillaud, et al.
La Tunisie Medicale
|
February 17, 2009
[Respiratory distress in infants with Pompe's disease]
Monia Khémiri, Marouene Zayani, Olfa Bou Yahya, et al.
Journal of Neurology
|
February 26, 2008
The pulvinar sign: frequency and clinical correlations in Fabry disease
Alessandro P Burlina, Renzo Manara, Catherine Caillaud, et al.
BMC Medical Genetics
|
June 28, 2020
First phenotypic description of a female patient with c.610 T > C variant of GLA: a renal-predominant presentation of Fabry disease
Sophie Greillier, Laurent Daniel, Catherine Caillaud, et al.
Journal of Inherited Metabolic Disease
|
June 29, 2023
Natural history of GM1 gangliosidosis-Retrospective cohort study of 61 French patients from 1998 to 2019
Domitille Laur, Samia Pichard, Soumeya Bekri, et al.
Molecular Genetics and Metabolism
|
November 26, 2015
Obstructive sleep apnea syndrome after hematopoietic stem cell transplantation in children with mucopolysaccharidosis type I
Johan Moreau, Anais Brassier, Alessandro Amaddeo, et al.
American Journal of Medical Genetics. Part A
|
May 1, 2019
Sleep-disordered breathing in children with mucolipidosis
Laurence Tabone, Catherine Caillaud, Alessandro Amaddeo, et al.
Page
of 9
Search research articles
Search
Showing results (21-30 of 86) with videos related to
Sort By:
Page
of 9
Neurobiology of Disease
|
December 17, 2009
Induced secretion of beta-hexosaminidase by human brain endothelial cells: a novel approach in Sandhoff disease?
Lionel Batista, Florence Miller, Céline Clave, et al.
Orphanet Journal of Rare Diseases
|
July 2, 2014
Modeling changes in biomarkers in Gaucher disease patients receiving enzyme replacement therapy using a pathophysiological model
Marie Vigan, Jérôme Stirnemann, Catherine Caillaud, et al.
American Journal of Medical Genetics. Part A
|
November 18, 2008
Developmental delay, dysmorphic features, neonatal spontaneous fractures, wrinkled skin, and hepatic failure: a new metabolic syndrome?
André Mégarbané, Leila Samaras, Rima Chédid, et al.
Neuromuscular Disorders : NMD
|
December 17, 2009
Rigid spine syndrome revealing late-onset Pompe disease
Pascal Laforêt, Valérie Doppler, Catherine Caillaud, et al.
La Tunisie Medicale
|
February 17, 2009
[Respiratory distress in infants with Pompe's disease]
Monia Khémiri, Marouene Zayani, Olfa Bou Yahya, et al.
Journal of Neurology
|
February 26, 2008
The pulvinar sign: frequency and clinical correlations in Fabry disease
Alessandro P Burlina, Renzo Manara, Catherine Caillaud, et al.
BMC Medical Genetics
|
June 28, 2020
First phenotypic description of a female patient with c.610 T > C variant of GLA: a renal-predominant presentation of Fabry disease
Sophie Greillier, Laurent Daniel, Catherine Caillaud, et al.
Journal of Inherited Metabolic Disease
|
June 29, 2023
Natural history of GM1 gangliosidosis-Retrospective cohort study of 61 French patients from 1998 to 2019
Domitille Laur, Samia Pichard, Soumeya Bekri, et al.
Molecular Genetics and Metabolism
|
November 26, 2015
Obstructive sleep apnea syndrome after hematopoietic stem cell transplantation in children with mucopolysaccharidosis type I
Johan Moreau, Anais Brassier, Alessandro Amaddeo, et al.
American Journal of Medical Genetics. Part A
|
May 1, 2019
Sleep-disordered breathing in children with mucolipidosis
Laurence Tabone, Catherine Caillaud, Alessandro Amaddeo, et al.
Page
of 9