Showing results (1-10 of 11) with videos related to

Sort By:
Pageof 2
Annals of Clinical and Translational Neurology|September 16, 2020
Adeno-associated virus serotype 1-based gene therapy for FTD caused by GRN mutationsChristian Hinderer, Rod Miller, Cecilia Dyer, et al.
Molecular Therapy. Methods & Clinical Development|May 19, 2020
Translational Feasibility of Lumbar Puncture for Intrathecal AAV AdministrationChristian Hinderer, Nathan Katz, Cecilia Dyer, et al.
Human Gene Therapy|January 31, 2018
Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMNChristian Hinderer, Nathan Katz, Elizabeth L Buza, et al.
Human Gene Therapy|January 31, 2023
Neonatal Fc Receptor Inhibition Enables Adeno-Associated Virus Gene Therapy Despite Pre-Existing Humoral ImmunityMakoto Horiuchi, Christian J Hinderer, Hailey N Shankle, et al.
Molecular Therapy. Methods & Clinical Development|November 24, 2022
Erratum: Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectorsMakoto Horiuchi, Christian J Hinderer, Jenny A Greig, et al.
Molecular Therapy. Methods & Clinical Development|November 2, 2022
Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectorsMakoto Horiuchi, Christian J Hinderer, Jenny A Greig, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|February 8, 2024
High-dose systemic adeno-associated virus vector administration causes liver and sinusoidal endothelial cell injuryJuliette Hordeaux, R Jason Lamontagne, Chunjuan Song, et al.
Human Gene Therapy|March 25, 2022
Efficacy and Safety of a Krabbe Disease Gene TherapyJuliette Hordeaux, Brianne A Jeffrey, Jinlong Jian, et al.
Frontiers in Immunology|April 10, 2023
Immune transgene-dependent myocarditis in macaques after systemic administration of adeno-associated virus expressing human acid alpha-glucosidaseJuliette Hordeaux, Ali Ramezani, Steve Tuske, et al.
Plos Pathogens|July 15, 2021
Intranasal gene therapy to prevent infection by SARS-CoV-2 variantsJoshua J Sims, Jenny A Greig, Kristofer T Michalson, et al.
Pageof 2