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Chiara Cimmaruta

Showing results (1-10 of 13) with videos related to

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Antioxidants & Redox Signaling|August 25, 2021
Reactive Species in Progeroid Syndromes and Aging-Related ProcessesClément Crochemore, Chiara Cimmaruta, Cristina Fernández-Molina, et al.
International Journal of Molecular Sciences|September 27, 2017
E-Learning for Rare Diseases: An Example Using Fabry DiseaseChiara Cimmaruta, Ludovica Liguori, Maria Monticelli, et al.
Biology of the Cell|February 28, 2026
A Robust Methodological Framework for Generating Whole-Brain and Cortical Organoids From Diverse Healthy- and Patient-Derived Induced Pluripotent Stem Cell LinesTara Fournier, Eugenia Pugliese, Benjamin Montagne, et al.
Plos One|December 21, 2017
A mutant of phosphomannomutase1 retains full enzymatic activity, but is not activated by IMP: Possible implications for the disease PMM2-CDGValentina Citro, Chiara Cimmaruta, Ludovica Liguori, et al.
BMC Bioinformatics|December 1, 2018
Challenging popular tools for the annotation of genetic variations with a real case, pathogenic mutations of lysosomal alpha-galactosidaseChiara Cimmaruta, Valentina Citro, Giuseppina Andreotti, et al.
International Journal of Molecular Sciences|December 6, 2016
The Large Phenotypic Spectrum of Fabry Disease Requires Graduated Diagnosis and Personalized Therapy: A Meta-Analysis Can Help to Differentiate Missense MutationsValentina Citro, Marco Cammisa, Ludovica Liguori, et al.
International Journal of Molecular Sciences|August 1, 2018
The Analysis of Variants in the General Population Reveals That <i>PMM2</i> Is Extremely Tolerant to Missense Mutations and That Diagnosis of PMM2-CDG Can Benefit from the Identification of ModifiersValentina Citro, Chiara Cimmaruta, Maria Monticelli, et al.
International Journal of Molecular Sciences|March 11, 2023
Enzyme Replacement Therapy for FABRY Disease: Possible Strategies to Improve Its EfficacyIlaria Iacobucci, Bruno Hay Mele, Flora Cozzolino, et al.
Stem Cell Research|November 1, 2019
Generation of the Niemann-Pick type C2 patient-derived iPSC line AKOSi001-AChristin Völkner, Franziska Peter, Maik Liedtke, et al.
International Journal of Molecular Sciences|February 7, 2020
Assessment of Gene Variant Amenability for Pharmacological Chaperone Therapy with 1-Deoxygalactonojirimycin in Fabry DiseaseJan Lukas, Chiara Cimmaruta, Ludovica Liguori, et al.
Pageof 2

Showing results (1-10 of 13) with videos related to

Sort By:
Pageof 2
Antioxidants & Redox Signaling|August 25, 2021
Reactive Species in Progeroid Syndromes and Aging-Related ProcessesClément Crochemore, Chiara Cimmaruta, Cristina Fernández-Molina, et al.
International Journal of Molecular Sciences|September 27, 2017
E-Learning for Rare Diseases: An Example Using Fabry DiseaseChiara Cimmaruta, Ludovica Liguori, Maria Monticelli, et al.
Biology of the Cell|February 28, 2026
A Robust Methodological Framework for Generating Whole-Brain and Cortical Organoids From Diverse Healthy- and Patient-Derived Induced Pluripotent Stem Cell LinesTara Fournier, Eugenia Pugliese, Benjamin Montagne, et al.
Plos One|December 21, 2017
A mutant of phosphomannomutase1 retains full enzymatic activity, but is not activated by IMP: Possible implications for the disease PMM2-CDGValentina Citro, Chiara Cimmaruta, Ludovica Liguori, et al.
BMC Bioinformatics|December 1, 2018
Challenging popular tools for the annotation of genetic variations with a real case, pathogenic mutations of lysosomal alpha-galactosidaseChiara Cimmaruta, Valentina Citro, Giuseppina Andreotti, et al.
International Journal of Molecular Sciences|December 6, 2016
The Large Phenotypic Spectrum of Fabry Disease Requires Graduated Diagnosis and Personalized Therapy: A Meta-Analysis Can Help to Differentiate Missense MutationsValentina Citro, Marco Cammisa, Ludovica Liguori, et al.
International Journal of Molecular Sciences|August 1, 2018
The Analysis of Variants in the General Population Reveals That <i>PMM2</i> Is Extremely Tolerant to Missense Mutations and That Diagnosis of PMM2-CDG Can Benefit from the Identification of ModifiersValentina Citro, Chiara Cimmaruta, Maria Monticelli, et al.
International Journal of Molecular Sciences|March 11, 2023
Enzyme Replacement Therapy for FABRY Disease: Possible Strategies to Improve Its EfficacyIlaria Iacobucci, Bruno Hay Mele, Flora Cozzolino, et al.
Stem Cell Research|November 1, 2019
Generation of the Niemann-Pick type C2 patient-derived iPSC line AKOSi001-AChristin Völkner, Franziska Peter, Maik Liedtke, et al.
International Journal of Molecular Sciences|February 7, 2020
Assessment of Gene Variant Amenability for Pharmacological Chaperone Therapy with 1-Deoxygalactonojirimycin in Fabry DiseaseJan Lukas, Chiara Cimmaruta, Ludovica Liguori, et al.
Pageof 2