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Biomed Research International
|
January 7, 2014
Biodistribution and molecular studies on orally administered nanoparticle-AON complexes encapsulated with alginate aiming at inducing dystrophin rescue in mdx mice
Maria Sofia Falzarano, Chiara Passarelli, Elena Bassi, et al.
European Journal of Human Genetics : EJHG
|
April 21, 2026
Revisiting LSDMCA: male lethality escape and genotype-phenotype correlations
Alfonso Manuel D'Alessio, Alessia Indrieri, Giuseppina Vitiello, et al.
Frontiers in Genetics
|
July 15, 2022
Genetics of Inherited Retinal Diseases in Understudied Ethnic Groups in Italian Hospitals
Paolo Enrico Maltese, Leonardo Colombo, Salvatore Martella, et al.
RMD Open
|
May 13, 2026
Clinical phenotype and laboratory markers in patients affected by haploinsufficiency of A20 (HA20): a case series from two Italian centres
Laura De Nardi, Silvia Federici, Eleonora De Martino, et al.
Biochimica Et Biophysica Acta. Gene Regulatory Mechanisms
|
September 5, 2017
Transcriptional and epigenetic analyses of the DMD locus reveal novel cis‑acting DNA elements that govern muscle dystrophin expression
Samuele Gherardi, Matteo Bovolenta, Chiara Passarelli, et al.
Frontiers in Immunology
|
June 26, 2026
Unexpected genetically determined immune dysregulation with liver involvement: GIMAP5 therapeutic dilemmas between targeted therapy and HSCT
Mattia Moratti, Michele La Manna, Lucia Colucci, et al.
Annals of Neurology
|
October 31, 2012
DPM2-CDG: a muscular dystrophy-dystroglycanopathy syndrome with severe epilepsy
Rita Barone, Chiara Aiello, Valérie Race, et al.
Journal of Clinical Immunology
|
May 31, 2019
Efficacy and Adverse Events During Janus Kinase Inhibitor Treatment of SAVI Syndrome
Stefano Volpi, Antonella Insalaco, Roberta Caorsi, et al.
Journal of Neurology, Neurosurgery, and Psychiatry
|
December 6, 2014
Validation of genetic modifiers for Duchenne muscular dystrophy: a multicentre study assessing SPP1 and LTBP4 variants
Janneke C van den Bergen, Monika Hiller, Stefan Böhringer, et al.
Nature Medicine
|
August 11, 2014
Translation from a DMD exon 5 IRES results in a functional dystrophin isoform that attenuates dystrophinopathy in humans and mice
Nicolas Wein, Adeline Vulin, Maria S Falzarano, et al.
Page
of 5
Search research articles
Search
Showing results (31-40 of 45) with videos related to
Sort By:
Page
of 5
Biomed Research International
|
January 7, 2014
Biodistribution and molecular studies on orally administered nanoparticle-AON complexes encapsulated with alginate aiming at inducing dystrophin rescue in mdx mice
Maria Sofia Falzarano, Chiara Passarelli, Elena Bassi, et al.
European Journal of Human Genetics : EJHG
|
April 21, 2026
Revisiting LSDMCA: male lethality escape and genotype-phenotype correlations
Alfonso Manuel D'Alessio, Alessia Indrieri, Giuseppina Vitiello, et al.
Frontiers in Genetics
|
July 15, 2022
Genetics of Inherited Retinal Diseases in Understudied Ethnic Groups in Italian Hospitals
Paolo Enrico Maltese, Leonardo Colombo, Salvatore Martella, et al.
RMD Open
|
May 13, 2026
Clinical phenotype and laboratory markers in patients affected by haploinsufficiency of A20 (HA20): a case series from two Italian centres
Laura De Nardi, Silvia Federici, Eleonora De Martino, et al.
Biochimica Et Biophysica Acta. Gene Regulatory Mechanisms
|
September 5, 2017
Transcriptional and epigenetic analyses of the DMD locus reveal novel cis‑acting DNA elements that govern muscle dystrophin expression
Samuele Gherardi, Matteo Bovolenta, Chiara Passarelli, et al.
Frontiers in Immunology
|
June 26, 2026
Unexpected genetically determined immune dysregulation with liver involvement: GIMAP5 therapeutic dilemmas between targeted therapy and HSCT
Mattia Moratti, Michele La Manna, Lucia Colucci, et al.
Annals of Neurology
|
October 31, 2012
DPM2-CDG: a muscular dystrophy-dystroglycanopathy syndrome with severe epilepsy
Rita Barone, Chiara Aiello, Valérie Race, et al.
Journal of Clinical Immunology
|
May 31, 2019
Efficacy and Adverse Events During Janus Kinase Inhibitor Treatment of SAVI Syndrome
Stefano Volpi, Antonella Insalaco, Roberta Caorsi, et al.
Journal of Neurology, Neurosurgery, and Psychiatry
|
December 6, 2014
Validation of genetic modifiers for Duchenne muscular dystrophy: a multicentre study assessing SPP1 and LTBP4 variants
Janneke C van den Bergen, Monika Hiller, Stefan Böhringer, et al.
Nature Medicine
|
August 11, 2014
Translation from a DMD exon 5 IRES results in a functional dystrophin isoform that attenuates dystrophinopathy in humans and mice
Nicolas Wein, Adeline Vulin, Maria S Falzarano, et al.
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of 5