Showing results (21-30 of 62) with videos related to

Sort By:
Pageof 7
Journal of Inherited Metabolic Disease|March 6, 2019
Enzyme replacement therapy outcomes across the disease spectrum: Findings from the mucopolysaccharidosis VI Clinical Surveillance ProgramPaul R Harmatz, Christina Lampe, Rossella Parini, et al.
Molecular Genetics and Metabolism|May 17, 2025
Long-term enzyme replacement therapy: Findings from the mucopolysaccharidosis VI clinical surveillance program after 15 years follow-upBarbara K Burton, Paul R Harmatz, Veronika Horvathova, et al.
Plos One|September 10, 2016
Heart and Cardiovascular Involvement in Patients with Mucopolysaccharidosis Type IVA (Morquio-A Syndrome)Christoph Kampmann, Tariq Abu-Tair, Seyfullah Gökce, et al.
Child'S Nervous System : Chns : Official Journal of the International Society for Pediatric Neurosurgery|May 28, 2018
Spinal cord issues in adult patients with MPS: transition of care surveyKemel A Ghotme, Fernando Alvarado-Gomez, Christina Lampe, et al.
Journal of Inherited Metabolic Disease|November 21, 2024
Development of a novel tool for individual treatment trials in mucopolysaccharidosisAnna-Maria Wiesinger, Brian Bigger, Roberto Giugliani, et al.
Orphanet Journal of Rare Diseases|May 10, 2022
Consensus statement on enzyme replacement therapy for mucopolysaccharidosis IVA in Central and South-Eastern European countriesMartin Magner, Zsuzsanna Almássy, Zoran Gucev, et al.
Plos Pathogens|August 14, 2023
A conserved microtubule-binding region in Xanthomonas XopL is indispensable for induced plant cell death reactionsSimon Ortmann, Jolina Marx, Christina Lampe, et al.
Pharmaceutics|May 27, 2023
An Innovative Tool for Evidence-Based, Personalized Treatment Trials in MucopolysaccharidosisAnna-Maria Wiesinger, Brian Bigger, Roberto Giugliani, et al.
Fortschritte Der Neurologie-Psychiatrie|April 27, 2021
[Home infusion therapy for Pompe disease: Recommendations for German-speaking countries]Andreas Hahn, Christina Lampe, Matthias Boentert, et al.
Pageof 7