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March 9, 2016
Impaired antibacterial autophagy links granulomatous intestinal inflammation in Niemann-Pick disease type C1 and XIAP deficiency with NOD2 variants in Crohn's disease
Tobias Schwerd, Sumeet Pandey, Huei-Ting Yang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 15, 2022
Replication competent retrovirus testing (RCR) in the National Gene Vector Biorepository: No evidence of RCR in 1,595 post-treatment peripheral blood samples obtained from 60 clinical trials
Kenneth Cornetta, Jing Yao, Kimberley House, et al.
The New England Journal of Medicine
|
April 30, 2025
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1
Claire Booth, Julián Sevilla, Elena Almarza, et al.
Obstetrical & Gynecological Survey
|
December 30, 2025
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1
Claire Booth, Julián Sevilla, Elena Almarza, et al.
The New England Journal of Medicine
|
October 15, 2025
Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency
Claire Booth, Katelyn Masiuk, Konstantinos Vazouras, et al.
Blood
|
July 14, 2012
Outcome of hematopoietic stem cell transplantation for adenosine deaminase-deficient severe combined immunodeficiency
Amel Hassan, Claire Booth, Alex Brightwell, et al.
Blood
|
September 9, 2020
Absent B cells, agammaglobulinemia, and hypertrophic cardiomyopathy in folliculin-interacting protein 1 deficiency
Francesco Saettini, Cecilia Poli, Jaime Vengoechea, et al.
Nature Medicine
|
January 29, 2020
Lentiviral gene therapy for X-linked chronic granulomatous disease
Donald B Kohn, Claire Booth, Elizabeth M Kang, et al.
Journal of Clinical Immunology
|
July 9, 2020
Neuroinflammatory Disease as an Isolated Manifestation of Hemophagocytic Lymphohistiocytosis
Annaliesse Blincoe, Maximilian Heeg, Patrick K Campbell, et al.
Blood
|
October 8, 2010
X-linked lymphoproliferative disease due to SAP/SH2D1A deficiency: a multicenter study on the manifestations, management and outcome of the disease
Claire Booth, Kimberly C Gilmour, Paul Veys, et al.
Page
of 9
Search research articles
Search
Showing results (71-80 of 89) with videos related to
Sort By:
Page
of 9
Gut
|
March 9, 2016
Impaired antibacterial autophagy links granulomatous intestinal inflammation in Niemann-Pick disease type C1 and XIAP deficiency with NOD2 variants in Crohn's disease
Tobias Schwerd, Sumeet Pandey, Huei-Ting Yang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 15, 2022
Replication competent retrovirus testing (RCR) in the National Gene Vector Biorepository: No evidence of RCR in 1,595 post-treatment peripheral blood samples obtained from 60 clinical trials
Kenneth Cornetta, Jing Yao, Kimberley House, et al.
The New England Journal of Medicine
|
April 30, 2025
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1
Claire Booth, Julián Sevilla, Elena Almarza, et al.
Obstetrical & Gynecological Survey
|
December 30, 2025
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1
Claire Booth, Julián Sevilla, Elena Almarza, et al.
The New England Journal of Medicine
|
October 15, 2025
Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency
Claire Booth, Katelyn Masiuk, Konstantinos Vazouras, et al.
Blood
|
July 14, 2012
Outcome of hematopoietic stem cell transplantation for adenosine deaminase-deficient severe combined immunodeficiency
Amel Hassan, Claire Booth, Alex Brightwell, et al.
Blood
|
September 9, 2020
Absent B cells, agammaglobulinemia, and hypertrophic cardiomyopathy in folliculin-interacting protein 1 deficiency
Francesco Saettini, Cecilia Poli, Jaime Vengoechea, et al.
Nature Medicine
|
January 29, 2020
Lentiviral gene therapy for X-linked chronic granulomatous disease
Donald B Kohn, Claire Booth, Elizabeth M Kang, et al.
Journal of Clinical Immunology
|
July 9, 2020
Neuroinflammatory Disease as an Isolated Manifestation of Hemophagocytic Lymphohistiocytosis
Annaliesse Blincoe, Maximilian Heeg, Patrick K Campbell, et al.
Blood
|
October 8, 2010
X-linked lymphoproliferative disease due to SAP/SH2D1A deficiency: a multicenter study on the manifestations, management and outcome of the disease
Claire Booth, Kimberly C Gilmour, Paul Veys, et al.
Page
of 9