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Claudio Bruno

Showing results (181-190 of 302) with videos related to

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European Journal of Human Genetics : EJHG|January 4, 2024
DAG1 haploinsufficiency is associated with sporadic and familial isolated or pauci-symptomatic hyperCKemiaMonica Traverso, Serena Baratto, Michele Iacomino, et al.
Orphanet Journal of Rare Diseases|May 14, 2017
Neutral Lipid Storage Diseases: clinical/genetic features and natural history in a large cohort of Italian patientsElena Maria Pennisi, Marcello Arca, Enrico Bertini, et al.
Science Translational Medicine|March 1, 2023
Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophyValentina Taglietti, Kaouthar Kefi, Lea Rivera, et al.
Nature Genetics|September 5, 2006
Deficiency of hyccin, a newly identified membrane protein, causes hypomyelination and congenital cataractFederico Zara, Roberta Biancheri, Claudio Bruno, et al.
Muscle & Nerve|October 23, 2021
An integrated approach to the evaluation of patients with asymptomatic or minimally symptomatic hyperCKemiaChiara Gemelli, Monica Traverso, Lucia Trevisan, et al.
Neurology|June 27, 2025
Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient CohortsAmy Pasternak, Michael P McDermott, Jacqueline Montes, et al.
European Journal of Medicinal Chemistry|June 9, 2016
Synthesis, antiarrhythmic activity, and toxicological evaluation of mexiletine analoguesMariagrazia Roselli, Alessia Carocci, Roberta Budriesi, et al.
Orphanet Journal of Rare Diseases|October 15, 2020
Creation and implementation of a European registry for patients with McArdle disease and other muscle glycogenoses (EUROMAC registry)Tomàs Pinós, Antoni L Andreu, Claudio Bruno, et al.
Vaccine|September 17, 2014
Vaccination recommendations for patients with neuromuscular diseaseSusanna Esposito, Claudio Bruno, Angela Berardinelli, et al.
Molecular Genetics & Genomic Medicine|August 7, 2025
Functional Characterization of a Novel Intronic Variant in PIEZO2 in a Recessive Form of Distal Arthrogryposis With Impaired Proprioception and Touch (DAIPT)Michela Bellardita, Ferruccio Romano, Ludovica Menta, et al.
Pageof 31

Showing results (181-190 of 302) with videos related to

Sort By:
Pageof 31
European Journal of Human Genetics : EJHG|January 4, 2024
DAG1 haploinsufficiency is associated with sporadic and familial isolated or pauci-symptomatic hyperCKemiaMonica Traverso, Serena Baratto, Michele Iacomino, et al.
Orphanet Journal of Rare Diseases|May 14, 2017
Neutral Lipid Storage Diseases: clinical/genetic features and natural history in a large cohort of Italian patientsElena Maria Pennisi, Marcello Arca, Enrico Bertini, et al.
Science Translational Medicine|March 1, 2023
Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophyValentina Taglietti, Kaouthar Kefi, Lea Rivera, et al.
Nature Genetics|September 5, 2006
Deficiency of hyccin, a newly identified membrane protein, causes hypomyelination and congenital cataractFederico Zara, Roberta Biancheri, Claudio Bruno, et al.
Muscle & Nerve|October 23, 2021
An integrated approach to the evaluation of patients with asymptomatic or minimally symptomatic hyperCKemiaChiara Gemelli, Monica Traverso, Lucia Trevisan, et al.
Neurology|June 27, 2025
Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient CohortsAmy Pasternak, Michael P McDermott, Jacqueline Montes, et al.
European Journal of Medicinal Chemistry|June 9, 2016
Synthesis, antiarrhythmic activity, and toxicological evaluation of mexiletine analoguesMariagrazia Roselli, Alessia Carocci, Roberta Budriesi, et al.
Orphanet Journal of Rare Diseases|October 15, 2020
Creation and implementation of a European registry for patients with McArdle disease and other muscle glycogenoses (EUROMAC registry)Tomàs Pinós, Antoni L Andreu, Claudio Bruno, et al.
Vaccine|September 17, 2014
Vaccination recommendations for patients with neuromuscular diseaseSusanna Esposito, Claudio Bruno, Angela Berardinelli, et al.
Molecular Genetics & Genomic Medicine|August 7, 2025
Functional Characterization of a Novel Intronic Variant in PIEZO2 in a Recessive Form of Distal Arthrogryposis With Impaired Proprioception and Touch (DAIPT)Michela Bellardita, Ferruccio Romano, Ludovica Menta, et al.
Pageof 31