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Methods in Molecular Biology (Clifton, N.J.)|January 2, 2023
Delivering Base Editors In Vivo by Adeno-Associated Virus VectorsColin K W Lim, Angelo J Miskalis, Pablo Perez-Pinera, et al.Biorxiv : the Preprint Server for Biology|January 3, 2024
A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTDTristan X McCallister, Colin K W Lim, William M Terpstra, et al.Science Advances|January 19, 2022
Targeted gene silencing in the nervous system with CRISPR-Cas13Jackson E Powell, Colin K W Lim, Ramya Krishnan, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|January 29, 2020
Treatment of a Mouse Model of ALS by In Vivo Base EditingColin K W Lim, Michael Gapinske, Alexandra K Brooks, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|August 15, 2022
CRISPR base editing of cis-regulatory elements enables the perturbation of neurodegeneration-linked genesColin K W Lim, Tristan X McCallister, Christian Saporito-Magriña, et al.Nature Communications|January 8, 2025
A high-fidelity CRISPR-Cas13 system improves abnormalities associated with C9ORF72-linked ALS/FTDTristan X McCallister, Colin K W Lim, Mayuri Singh, et al.Biorxiv : the Preprint Server for Biology|July 15, 2024
In vivo CRISPR base editing for treatment of Huntington's diseaseShraddha Shirguppe, Michael Gapinske, Devyani Swami, et al.Biorxiv : the Preprint Server for Biology|January 9, 2026
Treatment of Huntington's disease with a pan-HTT-targeting CRISPR nucleaseKatherine Tan, Daniela Del Bosque Siller, Alisha Y Xiong, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|April 26, 2026
Treatment of Huntington's disease with a pan-HTT-targeting CRISPR nucleaseKatherine Tan, Daniela Del Bosque Siller, Alisha Y Xiong, et al.Nature Biomedical Engineering|July 29, 2026
In vivo CRISPR base editing for treatment of Huntington's diseaseShraddha Shirguppe, Michael Gapinske, Devyani Swami, et al.Pageof 1