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Human Gene Therapy
|
April 2, 2015
Gene therapy for inherited diseases of liver metabolism
Pasquale Piccolo, Nicola Brunetti-Pierri
Journal of Inherited Metabolic Disease
|
May 19, 2023
Gene therapies for mucopolysaccharidoses
Alessandro Rossi, Nicola Brunetti-Pierri
Human Gene Therapy
|
December 23, 2024
Current and Emerging Issues in Adeno-Associated Virus Vector-Mediated Liver-Directed Gene Therapy
Pasquale Piccolo, Nicola Brunetti-Pierri
Essays in Biochemistry
|
June 11, 2010
Mitochondrial metabolite transport
Ferdinando Palmieri, Ciro Leonardo Pierri
Human Molecular Genetics
|
April 8, 2011
Helper-dependent adenoviral vectors for liver-directed gene therapy
Nicola Brunetti-Pierri, Philip Ng
Molecular Genetics and Metabolism
|
June 6, 2008
GM1 gangliosidosis: review of clinical, molecular, and therapeutic aspects
Nicola Brunetti-Pierri, Fernando Scaglia
European Journal of Medical Genetics
|
September 25, 2012
Focal congenital lipoatrophy and vascular malformation: a mild form of inverse Klippel-Trenaunay syndrome?
Gerarda Cappuccio, Nicola Brunetti-Pierri
Journal of Genetic Syndromes & Gene Therapy
|
June 3, 2014
Adenoviral Vectors for Hemophilia Gene Therapy
N Brunetti-Pierri, Philip Ng
Biomedicines
|
May 27, 2017
Challenges and Prospects for Helper-Dependent Adenoviral Vector-Mediated Gene Therapy
Pasquale Piccolo, Nicola Brunetti-Pierri
Virus Genes
|
June 9, 2017
Gene therapy with helper-dependent adenoviral vectors: lessons from studies in large animal models
Nicola Brunetti-Pierri, Philip Ng
Page
of 98
Search research articles
Search
Showing results (21-30 of 974) with videos related to
Sort By:
Page
of 98
Human Gene Therapy
|
April 2, 2015
Gene therapy for inherited diseases of liver metabolism
Pasquale Piccolo, Nicola Brunetti-Pierri
Journal of Inherited Metabolic Disease
|
May 19, 2023
Gene therapies for mucopolysaccharidoses
Alessandro Rossi, Nicola Brunetti-Pierri
Human Gene Therapy
|
December 23, 2024
Current and Emerging Issues in Adeno-Associated Virus Vector-Mediated Liver-Directed Gene Therapy
Pasquale Piccolo, Nicola Brunetti-Pierri
Essays in Biochemistry
|
June 11, 2010
Mitochondrial metabolite transport
Ferdinando Palmieri, Ciro Leonardo Pierri
Human Molecular Genetics
|
April 8, 2011
Helper-dependent adenoviral vectors for liver-directed gene therapy
Nicola Brunetti-Pierri, Philip Ng
Molecular Genetics and Metabolism
|
June 6, 2008
GM1 gangliosidosis: review of clinical, molecular, and therapeutic aspects
Nicola Brunetti-Pierri, Fernando Scaglia
European Journal of Medical Genetics
|
September 25, 2012
Focal congenital lipoatrophy and vascular malformation: a mild form of inverse Klippel-Trenaunay syndrome?
Gerarda Cappuccio, Nicola Brunetti-Pierri
Journal of Genetic Syndromes & Gene Therapy
|
June 3, 2014
Adenoviral Vectors for Hemophilia Gene Therapy
N Brunetti-Pierri, Philip Ng
Biomedicines
|
May 27, 2017
Challenges and Prospects for Helper-Dependent Adenoviral Vector-Mediated Gene Therapy
Pasquale Piccolo, Nicola Brunetti-Pierri
Virus Genes
|
June 9, 2017
Gene therapy with helper-dependent adenoviral vectors: lessons from studies in large animal models
Nicola Brunetti-Pierri, Philip Ng
Page
of 98