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Neuromuscular Disorders : NMD|November 5, 2021
Spinal muscular atrophy: from rags to richesEugenio Mercuri
Current Opinion in Pediatrics|November 19, 2013
Muscular dystrophy: new challenges and review of the current clinical trialsEugenio Mercuri, Francesco Muntoni
Developmental Medicine and Child Neurology|January 6, 2026
The floppy infant revisited: From bedside to genomeGianpaolo Cicala, Eugenio Mercuri
Lancet (London, England)|March 8, 2013
Muscular dystrophiesEugenio Mercuri, Francesco Muntoni
Annals of Neurology|July 26, 2012
The ever-expanding spectrum of congenital muscular dystrophiesEugenio Mercuri, Francesco Muntoni
Neurology|July 3, 2020
Suitability of external controls for drug evaluation in Duchenne muscular dystrophyNathalie Goemans, James Signorovitch, Gautam Sajeev, et al.
Current Opinion in Pediatrics|November 7, 2024
Treatment of spinal muscular atrophyMaria Carmela Pera, Eugenio Mercuri
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