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Brain : a Journal of Neurology
|
January 23, 2004
Frequency and phenotypic spectrum of ataxia with oculomotor apraxia 2: a clinical and genetic study in 18 patients
Isabelle Le Ber, Naïma Bouslam, Sophie Rivaud-Péchoux, et al.
Neuromuscular Disorders : NMD
|
December 14, 2007
Novel missense, insertion and deletion mutations in the neurotrophic tyrosine kinase receptor type 1 gene (NTRK1) associated with congenital insensitivity to pain with anhidrosis
Kathrin Huehne, Christiane Zweier, Klaus Raab, et al.
Journal of Medical Genetics
|
March 27, 2019
Pathogenic variants in the AFG3L2 proteolytic domain cause SCA28 through haploinsufficiency and proteostatic stress-driven OMA1 activation
Susanna Tulli, Andrea Del Bondio, Valentina Baderna, et al.
Annals of Neurology
|
May 23, 2008
Hereditary optic neuropathies share a common mitochondrial coupling defect
Arnaud Chevrollier, Virginie Guillet, Dominique Loiseau, et al.
Neurology. Genetics
|
February 24, 2018
AP4 deficiency: A novel form of neurodegeneration with brain iron accumulation?
Agathe Roubertie, Nelson Hieu, Charles-Joris Roux, et al.
European Journal of Medical Genetics
|
October 5, 2010
Lung disease associated with periventricular nodular heterotopia and an FLNA mutation
Alice Masurel-Paulet, Eric Haan, Elizabeth M Thompson, et al.
Haematologica
|
October 9, 2025
Expanded clinical, genetic, and biological spectrum of filaminopathies with hematological involvement
Charlotte Brillon, Marjorie Poggi, Mathieu Fiore, et al.
Orphanet Journal of Rare Diseases
|
October 9, 2015
Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: a retrospective case series analysis of nine sibships
Nouriya A Al-Sannaa, Luisa Bay, Deborah S Barbouth, et al.
Human Molecular Genetics
|
April 2, 2009
Five new TTF1/NKX2.1 mutations in brain-lung-thyroid syndrome: rescue by PAX8 synergism in one case
Aurore Carré, Gabor Szinnai, Mireille Castanet, et al.
Human Mutation
|
September 22, 2016
An Application of NGS for Molecular Investigations in Perrault Syndrome: Study of 14 Families and Review of the Literature
Justine Lerat, Laurence Jonard, Natalie Loundon, et al.
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Search research articles
Search
Showing results (71-80 of 173) with videos related to
Sort By:
Page
of 18
Brain : a Journal of Neurology
|
January 23, 2004
Frequency and phenotypic spectrum of ataxia with oculomotor apraxia 2: a clinical and genetic study in 18 patients
Isabelle Le Ber, Naïma Bouslam, Sophie Rivaud-Péchoux, et al.
Neuromuscular Disorders : NMD
|
December 14, 2007
Novel missense, insertion and deletion mutations in the neurotrophic tyrosine kinase receptor type 1 gene (NTRK1) associated with congenital insensitivity to pain with anhidrosis
Kathrin Huehne, Christiane Zweier, Klaus Raab, et al.
Journal of Medical Genetics
|
March 27, 2019
Pathogenic variants in the AFG3L2 proteolytic domain cause SCA28 through haploinsufficiency and proteostatic stress-driven OMA1 activation
Susanna Tulli, Andrea Del Bondio, Valentina Baderna, et al.
Annals of Neurology
|
May 23, 2008
Hereditary optic neuropathies share a common mitochondrial coupling defect
Arnaud Chevrollier, Virginie Guillet, Dominique Loiseau, et al.
Neurology. Genetics
|
February 24, 2018
AP4 deficiency: A novel form of neurodegeneration with brain iron accumulation?
Agathe Roubertie, Nelson Hieu, Charles-Joris Roux, et al.
European Journal of Medical Genetics
|
October 5, 2010
Lung disease associated with periventricular nodular heterotopia and an FLNA mutation
Alice Masurel-Paulet, Eric Haan, Elizabeth M Thompson, et al.
Haematologica
|
October 9, 2025
Expanded clinical, genetic, and biological spectrum of filaminopathies with hematological involvement
Charlotte Brillon, Marjorie Poggi, Mathieu Fiore, et al.
Orphanet Journal of Rare Diseases
|
October 9, 2015
Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: a retrospective case series analysis of nine sibships
Nouriya A Al-Sannaa, Luisa Bay, Deborah S Barbouth, et al.
Human Molecular Genetics
|
April 2, 2009
Five new TTF1/NKX2.1 mutations in brain-lung-thyroid syndrome: rescue by PAX8 synergism in one case
Aurore Carré, Gabor Szinnai, Mireille Castanet, et al.
Human Mutation
|
September 22, 2016
An Application of NGS for Molecular Investigations in Perrault Syndrome: Study of 14 Families and Review of the Literature
Justine Lerat, Laurence Jonard, Natalie Loundon, et al.
Page
of 18