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Molecular Therapy. Nucleic Acids|September 10, 2018
Priming Human Repopulating Hematopoietic Stem and Progenitor Cells for Cas9/sgRNA Gene TargetingCarsten T Charlesworth, Joab Camarena, M Kyle Cromer, et al.
Nucleic Acids Research|June 1, 2019
Highly efficient editing of the β-globin gene in patient-derived hematopoietic stem and progenitor cells to treat sickle cell diseaseSo Hyun Park, Ciaran M Lee, Daniel P Dever, et al.
Nature Communications|January 3, 2024
Transient inhibition of 53BP1 increases the frequency of targeted integration in human hematopoietic stem and progenitor cellsRon Baik, M Kyle Cromer, Steve E Glenn, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|July 15, 2018
Global Transcriptional Response to CRISPR/Cas9-AAV6-Based Genome Editing in CD34+ Hematopoietic Stem and Progenitor CellsM Kyle Cromer, Sriram Vaidyanathan, Daniel E Ryan, et al.
Nature|November 8, 2016
CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cellsDaniel P Dever, Rasmus O Bak, Andreas Reinisch, et al.
Iscience|May 28, 2019
CRISPR/Cas9 Genome Engineering in Engraftable Human Brain-Derived Neural Stem CellsDaniel P Dever, Samantha G Scharenberg, Joab Camarena, et al.
Molecular Therapy. Methods & Clinical Development|September 6, 2021
Clinically relevant gene editing in hematopoietic stem cells for the treatment of pyruvate kinase deficiencySara Fañanas-Baquero, Oscar Quintana-Bustamante, Daniel P Dever, et al.
Cell Stem Cell|May 4, 2019
Highly Efficient and Marker-free Genome Editing of Human Pluripotent Stem Cells by CRISPR-Cas9 RNP and AAV6 Donor-Mediated Homologous RecombinationRenata M Martin, Kazuya Ikeda, M Kyle Cromer, et al.
Nature Medicine|August 8, 2018
A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human hematopoietic stem and progenitor cellsChristopher A Vakulskas, Daniel P Dever, Garrett R Rettig, et al.
Science Translational Medicine|June 17, 2021
Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell diseaseAnnalisa Lattanzi, Joab Camarena, Premanjali Lahiri, et al.
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