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Journal of Hepatology
|
November 18, 2008
Glucose metabolism and diet-based prevention of liver dysfunction in MPV17 mutant patients
Rossella Parini, Francesca Furlan, Luigi Notarangelo, et al.
Orphanet Journal of Rare Diseases
|
September 19, 2014
Clinical efficacy of enzyme replacement therapy in paediatric Hunter patients, an independent study of 3.5 years
Rosella Tomanin, Alessandra Zanetti, Francesca D'Avanzo, et al.
Orphanet Journal of Rare Diseases
|
March 12, 2015
Long-term follow-up of patients with phenylketonuria treated with tetrahydrobiopterin: a seven years experience
Iris Scala, Daniela Concolino, Roberto Della Casa, et al.
Minerva Anestesiologica
|
December 15, 2017
Facing up to limits: a lesson from the Charlie Gard case
Alberto Giannini, Paola Cogo, Bruno Bembi, et al.
Oncotarget
|
January 4, 2018
Genetic variants associated with Fabry disease progression despite enzyme replacement therapy
Francesca Scionti, Maria Teresa Di Martino, Simona Sestito, et al.
American Journal of Human Genetics
|
December 17, 2009
Targeted next-generation sequencing appoints c16orf57 as clericuzio-type poikiloderma with neutropenia gene
Ludovica Volpi, Gaia Roversi, Elisa Adele Colombo, et al.
Stem Cell Research
|
September 7, 2019
Generation of three iPSC lines (IAIi002, IAIi004, IAIi003) from Rubinstein-Taybi syndrome 1 patients carrying CREBBP non sense c.4435G>T, p.(Gly1479*) and c.3474G>A, p.(Trp1158*) and missense c.4627G>T, p.(Asp1543Tyr) mutations
Valentina Alari, Silvia Russo, Davide Rovina, et al.
Italian Journal of Pediatrics
|
March 6, 2022
Immune responses to alglucosidase in infantile Pompe disease: recommendations from an Italian pediatric expert panel
Vincenza Gragnaniello, Federica Deodato, Serena Gasperini, et al.
Stem Cell Research
|
June 9, 2018
iPSC-derived neurons of CREBBP- and EP300-mutated Rubinstein-Taybi syndrome patients show morphological alterations and hypoexcitability
Valentina Alari, Silvia Russo, Benedetta Terragni, et al.
Clinica Chimica Acta; International Journal of Clinical Chemistry
|
August 16, 2018
False positive screen test for mucopolysaccharidoses in healthy female newborns
Chiara Monachesi, Lucia Zampini, Lucia Padella, et al.
Page
of 8
Search research articles
Search
Showing results (51-60 of 80) with videos related to
Sort By:
Page
of 8
Journal of Hepatology
|
November 18, 2008
Glucose metabolism and diet-based prevention of liver dysfunction in MPV17 mutant patients
Rossella Parini, Francesca Furlan, Luigi Notarangelo, et al.
Orphanet Journal of Rare Diseases
|
September 19, 2014
Clinical efficacy of enzyme replacement therapy in paediatric Hunter patients, an independent study of 3.5 years
Rosella Tomanin, Alessandra Zanetti, Francesca D'Avanzo, et al.
Orphanet Journal of Rare Diseases
|
March 12, 2015
Long-term follow-up of patients with phenylketonuria treated with tetrahydrobiopterin: a seven years experience
Iris Scala, Daniela Concolino, Roberto Della Casa, et al.
Minerva Anestesiologica
|
December 15, 2017
Facing up to limits: a lesson from the Charlie Gard case
Alberto Giannini, Paola Cogo, Bruno Bembi, et al.
Oncotarget
|
January 4, 2018
Genetic variants associated with Fabry disease progression despite enzyme replacement therapy
Francesca Scionti, Maria Teresa Di Martino, Simona Sestito, et al.
American Journal of Human Genetics
|
December 17, 2009
Targeted next-generation sequencing appoints c16orf57 as clericuzio-type poikiloderma with neutropenia gene
Ludovica Volpi, Gaia Roversi, Elisa Adele Colombo, et al.
Stem Cell Research
|
September 7, 2019
Generation of three iPSC lines (IAIi002, IAIi004, IAIi003) from Rubinstein-Taybi syndrome 1 patients carrying CREBBP non sense c.4435G>T, p.(Gly1479*) and c.3474G>A, p.(Trp1158*) and missense c.4627G>T, p.(Asp1543Tyr) mutations
Valentina Alari, Silvia Russo, Davide Rovina, et al.
Italian Journal of Pediatrics
|
March 6, 2022
Immune responses to alglucosidase in infantile Pompe disease: recommendations from an Italian pediatric expert panel
Vincenza Gragnaniello, Federica Deodato, Serena Gasperini, et al.
Stem Cell Research
|
June 9, 2018
iPSC-derived neurons of CREBBP- and EP300-mutated Rubinstein-Taybi syndrome patients show morphological alterations and hypoexcitability
Valentina Alari, Silvia Russo, Benedetta Terragni, et al.
Clinica Chimica Acta; International Journal of Clinical Chemistry
|
August 16, 2018
False positive screen test for mucopolysaccharidoses in healthy female newborns
Chiara Monachesi, Lucia Zampini, Lucia Padella, et al.
Page
of 8