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Neurology. Genetics|May 21, 2026
Ataxia With Vitamin E Deficiency Syndrome and a Novel TTPA Variant: A Paired Case ReportGiacomo Baso, Francesca Magri, Monica Sciacco, et al.
Neurology. Genetics|July 11, 2022
Expanding the Phenotypic Spectrum of Vocal Cord and Pharyngeal Weakness With Distal Myopathy due to the p.S85C MATR3 MutationArianna Manini, Daniele Velardo, Patrizia Ciscato, et al.
Neurology. Genetics|December 20, 2021
Homozygous SOD1 Variation L144S Produces a Severe Form of Amyotrophic Lateral Sclerosis in an Iranian FamilyDelia Gagliardi, Minoo Ahmadinejad, Roberto Del Bo, et al.
Journal of Personalized Medicine|January 21, 2023
MERRF Mutation A8344G in a Four-Generation Family without Central Nervous System Involvement: Clinical and Molecular CharacterizationMichela Ripolone, Simona Zanotti, Laura Napoli, et al.
Neurology Research International|June 20, 2013
Mitochondrial fusion proteins and human diseasesMichela Ranieri, Simona Brajkovic, Giulietta Riboldi, et al.
BMC Neurology|August 4, 2014
A novel CCM1 mutation associated with multiple cerebral and vertebral cavernous malformationsSilvia Lanfranconi, Dario Ronchi, Naghia Ahmed, et al.
Frontiers in Genetics|December 23, 2024
Case report: Multiple approach analysis in a case of clinically assessed myotonia congenitaSabrina Lucchiari, Francesco Fortunato, Giovanni Meola, et al.
Scientific Reports|February 24, 2023
NOTCH2NLC GGC repeats are not expanded in Italian amyotrophic lateral sclerosis patientsArianna Manini, Delia Gagliardi, Megi Meneri, et al.
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