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Molecular Genetics and Metabolism|January 14, 2014
Long-term nonsense suppression therapy moderates MPS I-H disease progressionGwen Gunn, Yanying Dai, Ming Du, et al.
The Journal of Infectious Diseases|June 11, 2013
Heterozygosity for the F508del mutation in the cystic fibrosis transmembrane conductance regulator anion channel attenuates influenza severityFamke Aeffner, Basant Abdulrahman, Judy M Hickman-Davis, et al.
Plos One|April 18, 2013
Attenuation of nonsense-mediated mRNA decay enhances in vivo nonsense suppressionKim M Keeling, Dan Wang, Yanying Dai, et al.
Journal of Cystic Fibrosis : Official Journal of the European Cystic Fibrosis Society|September 27, 2025
Identity, functional consequences, and context effects of amino acids inserted during suppression of CFTR nonsense mutationsKari Thrasher, Jianguo Chen, Lianwu Fu, et al.
American Journal of Physiology. Lung Cellular and Molecular Physiology|April 4, 2023
The synthetic aminoglycoside ELX-02 induces readthrough of G550X-CFTR producing superfunctional protein that can be further enhanced by CFTR modulatorsJianguo Chen, Kari Thrasher, Lianwu Fu, et al.
Journal of Molecular Medicine (Berlin, Germany)|July 23, 2011
Suppression of CFTR premature termination codons and rescue of CFTR protein and function by the synthetic aminoglycoside NB54Steven M Rowe, Peter Sloane, Li Ping Tang, et al.
Molecular Therapy. Nucleic Acids|May 15, 2020
Mutation-Directed Therapeutics for Neurofibromatosis Type IAndre Leier, David M Bedwell, Ann T Chen, et al.
Disease Models & Mechanisms|August 3, 2016
Mice with missense and nonsense NF1 mutations display divergent phenotypes compared with human neurofibromatosis type IKairong Li, Ashley N Turner, Min Chen, et al.
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