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Expert Opinion on Biological Therapy
|
February 24, 2023
Gene therapy for alpha-1 antitrypsin deficiency: an update
Debora Pires Ferreira, Alisha M Gruntman, Terence R Flotte
Human Gene Therapy
|
May 20, 2026
Optimization of Alpha-1 Antitrypsin Expression from Adeno-Associated Virus Vectors
Qiushi Tang, Debora Pires-Ferreira, Christian Mueller, et al.
Biorxiv : the Preprint Server for Biology
|
July 14, 2025
A Compact Base Editor Rescues AATD-associated Liver and Lung Disease in Mouse Models
Jenny Gao, Nathan Bamidele, Debora Pires-Ferreira, et al.
Molecular Therapy. Methods & Clinical Development
|
March 6, 2024
Biodistribution and safety of a single rAAV3B-AAT vector for silencing and replacement of alpha-1 antitrypsin in <i>Cynomolgus macaques</i>
Meghan Blackwood, Alisha M Gruntman, Qiushi Tang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
August 30, 2025
A Compact Base Editor Rescues AATD-associated Liver and Lung Disease in Mouse Models
Jenny Gao, Nathan Bamidele, Debora Pires-Ferreira, et al.
Genes
|
September 28, 2024
Limb Perfusion Delivery of a rAAV1 Alpha-1 Antitrypsin Vector in Non-Human Primates Is Safe but Insufficient for Therapy
Debora Pires-Ferreira, Darcy Reil, Qiushi Tang, et al.
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of 1
Search research articles
Search
Showing results (1-10 of 6) with videos related to
Sort By:
Page
of 1
Expert Opinion on Biological Therapy
|
February 24, 2023
Gene therapy for alpha-1 antitrypsin deficiency: an update
Debora Pires Ferreira, Alisha M Gruntman, Terence R Flotte
Human Gene Therapy
|
May 20, 2026
Optimization of Alpha-1 Antitrypsin Expression from Adeno-Associated Virus Vectors
Qiushi Tang, Debora Pires-Ferreira, Christian Mueller, et al.
Biorxiv : the Preprint Server for Biology
|
July 14, 2025
A Compact Base Editor Rescues AATD-associated Liver and Lung Disease in Mouse Models
Jenny Gao, Nathan Bamidele, Debora Pires-Ferreira, et al.
Molecular Therapy. Methods & Clinical Development
|
March 6, 2024
Biodistribution and safety of a single rAAV3B-AAT vector for silencing and replacement of alpha-1 antitrypsin in <i>Cynomolgus macaques</i>
Meghan Blackwood, Alisha M Gruntman, Qiushi Tang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
August 30, 2025
A Compact Base Editor Rescues AATD-associated Liver and Lung Disease in Mouse Models
Jenny Gao, Nathan Bamidele, Debora Pires-Ferreira, et al.
Genes
|
September 28, 2024
Limb Perfusion Delivery of a rAAV1 Alpha-1 Antitrypsin Vector in Non-Human Primates Is Safe but Insufficient for Therapy
Debora Pires-Ferreira, Darcy Reil, Qiushi Tang, et al.
Page
of 1