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Denise A Carbonaro

Showing results (1-10 of 15) with videos related to

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Journal of Clinical Immunology|August 27, 2017
Adenosine Deaminase (ADA)-Deficient Severe Combined Immune Deficiency (SCID): Molecular Pathogenesis and Clinical ManifestationsKathryn L Bradford, Federico A Moretti, Denise A Carbonaro-Sarracino, et al.
Molecular Therapy. Methods & Clinical Development|March 19, 2021
Gene delivery using AAV8 <i>in vivo</i> for disease stabilization in a bimodal gene therapy approach for the treatment of ADA-deficient SCIDDenise A Carbonaro-Sarracino, Krista Chun, Danielle N Clark, et al.
Blood|March 30, 2017
Cytoreductive conditioning intensity predicts clonal diversity in ADA-SCID retroviral gene therapy patientsAaron R Cooper, Georgia R Lill, Kit Shaw, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|May 3, 2006
In vivo transduction by intravenous injection of a lentiviral vector expressing human ADA into neonatal ADA gene knockout mice: a novel form of enzyme replacement therapy for ADA deficiencyDenise A Carbonaro, Xiangyang Jin, Denise Petersen, et al.
Nature Medicine|March 18, 2003
Clonality analysis after retroviral-mediated gene transfer to CD34+ cells from the cord blood of ADA-deficient SCID neonatesManfred Schmidt, Denise A Carbonaro, Carsten Speckmann, et al.
Blood|March 22, 2008
Neonatal bone marrow transplantation of ADA-deficient SCID mice results in immunologic reconstitution despite low levels of engraftment and an absence of selective donor T lymphoid expansionDenise A Carbonaro, Xiangyang Jin, Daniel Cotoi, et al.
Blood|July 27, 2012
Gene therapy/bone marrow transplantation in ADA-deficient mice: roles of enzyme-replacement therapy and cytoreductionDenise A Carbonaro, Xiangyang Jin, Xingchao Wang, et al.
Molecular Therapy. Methods & Clinical Development|December 25, 2019
Dosing and Re-Administration of Lentiviral Vector for <i>In Vivo</i> Gene Therapy in Rhesus Monkeys and ADA-Deficient MiceDenise A Carbonaro-Sarracino, Alice F Tarantal, C Chang I Lee, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|November 1, 2002
Expression from second-generation feline immunodeficiency virus vectors is impaired in human hematopoietic cellsMary A Price, Scott S Case, Denise A Carbonaro, et al.
Human Gene Therapy|September 10, 2016
Lentivirus Mediated Correction of Artemis-Deficient Severe Combined ImmunodeficiencyDivya Punwani, Misako Kawahara, Jason Yu, et al.
Pageof 2

Showing results (1-10 of 15) with videos related to

Sort By:
Pageof 2
Journal of Clinical Immunology|August 27, 2017
Adenosine Deaminase (ADA)-Deficient Severe Combined Immune Deficiency (SCID): Molecular Pathogenesis and Clinical ManifestationsKathryn L Bradford, Federico A Moretti, Denise A Carbonaro-Sarracino, et al.
Molecular Therapy. Methods & Clinical Development|March 19, 2021
Gene delivery using AAV8 <i>in vivo</i> for disease stabilization in a bimodal gene therapy approach for the treatment of ADA-deficient SCIDDenise A Carbonaro-Sarracino, Krista Chun, Danielle N Clark, et al.
Blood|March 30, 2017
Cytoreductive conditioning intensity predicts clonal diversity in ADA-SCID retroviral gene therapy patientsAaron R Cooper, Georgia R Lill, Kit Shaw, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|May 3, 2006
In vivo transduction by intravenous injection of a lentiviral vector expressing human ADA into neonatal ADA gene knockout mice: a novel form of enzyme replacement therapy for ADA deficiencyDenise A Carbonaro, Xiangyang Jin, Denise Petersen, et al.
Nature Medicine|March 18, 2003
Clonality analysis after retroviral-mediated gene transfer to CD34+ cells from the cord blood of ADA-deficient SCID neonatesManfred Schmidt, Denise A Carbonaro, Carsten Speckmann, et al.
Blood|March 22, 2008
Neonatal bone marrow transplantation of ADA-deficient SCID mice results in immunologic reconstitution despite low levels of engraftment and an absence of selective donor T lymphoid expansionDenise A Carbonaro, Xiangyang Jin, Daniel Cotoi, et al.
Blood|July 27, 2012
Gene therapy/bone marrow transplantation in ADA-deficient mice: roles of enzyme-replacement therapy and cytoreductionDenise A Carbonaro, Xiangyang Jin, Xingchao Wang, et al.
Molecular Therapy. Methods & Clinical Development|December 25, 2019
Dosing and Re-Administration of Lentiviral Vector for <i>In Vivo</i> Gene Therapy in Rhesus Monkeys and ADA-Deficient MiceDenise A Carbonaro-Sarracino, Alice F Tarantal, C Chang I Lee, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|November 1, 2002
Expression from second-generation feline immunodeficiency virus vectors is impaired in human hematopoietic cellsMary A Price, Scott S Case, Denise A Carbonaro, et al.
Human Gene Therapy|September 10, 2016
Lentivirus Mediated Correction of Artemis-Deficient Severe Combined ImmunodeficiencyDivya Punwani, Misako Kawahara, Jason Yu, et al.
Pageof 2