Showing results (231-240 of 299) with videos related to

Sort By:
Pageof 30
Molecular Therapy : the Journal of the American Society of Gene Therapy|November 18, 2010
Minicircle DNA-based gene therapy coupled with immune modulation permits long-term expression of α-L-iduronidase in mice with mucopolysaccharidosis type IMark J Osborn, Ron T McElmurry, Christopher J Lees, et al.
Molecular Therapy. Methods & Clinical Development|December 14, 2020
AAV vectors engineered to target insulin receptor greatly enhance intramuscular gene deliveryCody B Jackson, Audrey S Richard, Amrita Ojha, et al.
Science Translational Medicine|December 1, 2017
Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophyLeonela Amoasii, Chengzu Long, Hui Li, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|April 26, 2007
Correction of DNA protein kinase deficiency by spliceosome-mediated RNA trans-splicing and sleeping beauty transposon deliveryHatem Zayed, Lily Xia, Anton Yerich, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|April 5, 2008
The host response to adenovirus, helper-dependent adenovirus, and adeno-associated virus in mouse liverAnton P McCaffrey, Paul Fawcett, Hiroyuki Nakai, et al.
Scientific Reports|January 29, 2015
Novel codon-optimized mini-intronic plasmid for efficient, inexpensive, and xeno-free induction of pluripotencySebastian Diecke, Jiamiao Lu, Jaecheol Lee, et al.
Nucleic Acids Research|September 11, 2016
TALEN/CRISPR-mediated engineering of a promoterless anti-viral RNAi hairpin into an endogenous miRNA locusElena Senís, Stefan Mockenhaupt, Daniel Rupp, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|October 17, 2017
Survival Advantage of Both Human Hepatocyte Xenografts and Genome-Edited Hepatocytes for Treatment of α-1 Antitrypsin DeficiencyFlorie Borel, Qiushi Tang, Gwladys Gernoux, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|January 17, 2022
Ex vivo and in vivo suppression of SARS-CoV-2 with combinatorial AAV/RNAi expression vectorsJonas Becker, Megan Lynn Stanifer, Sarah Rebecca Leist, et al.
Viruses|March 6, 2021
Characterization of the GBoV1 Capsid and Its Antibody InteractionsJennifer Chun Yu, Mario Mietzsch, Amriti Singh, et al.
Pageof 30