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Donald B Kohn

Showing results (121-130 of 273) with videos related to

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Pediatric Transplantation|September 30, 2008
Clinical and genetic heterogeneity in Omenn syndrome and severe combined immune deficiencyTanja A Gruber, Ami J Shah, Michelle Hernandez, et al.
Stem Cell Reports|November 13, 2020
β-Globin Lentiviral Vectors Have Reduced Titers due to Incomplete Vector RNA Genomes and Lowered Virion ProductionJiaying Han, Kevin Tam, Feiyang Ma, et al.
Molecular Therapy. Methods & Clinical Development|May 15, 2024
A novel high-titer, bifunctional lentiviral vector for autologous hematopoietic stem cell gene therapy of sickle cell diseaseKevyn L Hart, Boya Liu, Devin Brown, et al.
Nature Medicine|March 18, 2003
Clonality analysis after retroviral-mediated gene transfer to CD34+ cells from the cord blood of ADA-deficient SCID neonatesManfred Schmidt, Denise A Carbonaro, Carsten Speckmann, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|May 3, 2006
In vivo transduction by intravenous injection of a lentiviral vector expressing human ADA into neonatal ADA gene knockout mice: a novel form of enzyme replacement therapy for ADA deficiencyDenise A Carbonaro, Xiangyang Jin, Denise Petersen, et al.
Biology of Blood and Marrow Transplantation : Journal of the American Society for Blood and Marrow Transplantation|April 24, 2007
The effects of Campath 1H upon graft-versus-host disease, infection, relapse, and immune reconstitution in recipients of pediatric unrelated transplantsAmi J Shah, Neena Kapoor, Gay M Crooks, et al.
Molecular Therapy. Methods & Clinical Development|December 12, 2018
Pre-clinical Development of a Lentiviral Vector Expressing the Anti-sickling βAS3 Globin for Gene Therapy for Sickle Cell DiseaseValentina Poletti, Fabrizia Urbinati, Sabine Charrier, et al.
Human Gene Therapy|September 11, 2018
Gene Therapy for Sickle Cell Disease: A Lentiviral Vector Comparison StudyFabrizia Urbinati, Beatriz Campo Fernandez, Katelyn E Masiuk, et al.
Proceedings of the National Academy of Sciences of the United States of America|January 16, 2013
Long-term in vivo monitoring of mouse and human hematopoietic stem cell engraftment with a human positron emission tomography reporter geneMelissa N McCracken, Eric H Gschweng, Evan Nair-Gill, et al.
Stem Cells (Dayton, Ohio)|March 3, 2016
Genetic Tagging During Human Mesoderm Differentiation Reveals Tripotent Lateral Plate Mesodermal ProgenitorsChee Jia Chin, Aaron R Cooper, Georgia R Lill, et al.
Pageof 28

Showing results (121-130 of 273) with videos related to

Sort By:
Pageof 28
Pediatric Transplantation|September 30, 2008
Clinical and genetic heterogeneity in Omenn syndrome and severe combined immune deficiencyTanja A Gruber, Ami J Shah, Michelle Hernandez, et al.
Stem Cell Reports|November 13, 2020
β-Globin Lentiviral Vectors Have Reduced Titers due to Incomplete Vector RNA Genomes and Lowered Virion ProductionJiaying Han, Kevin Tam, Feiyang Ma, et al.
Molecular Therapy. Methods & Clinical Development|May 15, 2024
A novel high-titer, bifunctional lentiviral vector for autologous hematopoietic stem cell gene therapy of sickle cell diseaseKevyn L Hart, Boya Liu, Devin Brown, et al.
Nature Medicine|March 18, 2003
Clonality analysis after retroviral-mediated gene transfer to CD34+ cells from the cord blood of ADA-deficient SCID neonatesManfred Schmidt, Denise A Carbonaro, Carsten Speckmann, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|May 3, 2006
In vivo transduction by intravenous injection of a lentiviral vector expressing human ADA into neonatal ADA gene knockout mice: a novel form of enzyme replacement therapy for ADA deficiencyDenise A Carbonaro, Xiangyang Jin, Denise Petersen, et al.
Biology of Blood and Marrow Transplantation : Journal of the American Society for Blood and Marrow Transplantation|April 24, 2007
The effects of Campath 1H upon graft-versus-host disease, infection, relapse, and immune reconstitution in recipients of pediatric unrelated transplantsAmi J Shah, Neena Kapoor, Gay M Crooks, et al.
Molecular Therapy. Methods & Clinical Development|December 12, 2018
Pre-clinical Development of a Lentiviral Vector Expressing the Anti-sickling βAS3 Globin for Gene Therapy for Sickle Cell DiseaseValentina Poletti, Fabrizia Urbinati, Sabine Charrier, et al.
Human Gene Therapy|September 11, 2018
Gene Therapy for Sickle Cell Disease: A Lentiviral Vector Comparison StudyFabrizia Urbinati, Beatriz Campo Fernandez, Katelyn E Masiuk, et al.
Proceedings of the National Academy of Sciences of the United States of America|January 16, 2013
Long-term in vivo monitoring of mouse and human hematopoietic stem cell engraftment with a human positron emission tomography reporter geneMelissa N McCracken, Eric H Gschweng, Evan Nair-Gill, et al.
Stem Cells (Dayton, Ohio)|March 3, 2016
Genetic Tagging During Human Mesoderm Differentiation Reveals Tripotent Lateral Plate Mesodermal ProgenitorsChee Jia Chin, Aaron R Cooper, Georgia R Lill, et al.
Pageof 28