Search research articles
Contact Us
Filters
Showing results (41-50 of 63) with videos related to
Page
of 7
Sort By:
Orphanet Journal of Rare Diseases
|
February 29, 2020
Lower plasma cholesterol, LDL-cholesterol and LDL-lipoprotein subclasses in adult phenylketonuria (PKU) patients compared to healthy controls: results of NMR metabolomics investigation
Claire Cannet, Andrea Pilotto, Júlio César Rocha, et al.
Journal of Child Neurology
|
December 29, 2012
Aspartylglucosaminuria: unusual neonatal presentation in Qatari twins with a novel aspartylglucosaminidase gene mutation and 3 new cases in a Turkish family
Thomas Opladen, Friedrich Ebinger, Johannes Zschocke, et al.
Nutrients
|
August 12, 2023
Combined Newborn Screening Allows Comprehensive Identification also of Attenuated Phenotypes for Methylmalonic Acidurias and Homocystinuria
Elena Schnabel, Stefan Kölker, Florian Gleich, et al.
Molecular Genetics and Metabolism
|
February 15, 2025
Kidney involvement in glycogen storage disease type I: Current knowledge and key challenges
Anke Schumann, Sven F Garbade, Skadi Beblo, et al.
European Journal of Human Genetics : EJHG
|
December 30, 2010
Mutation in mitochondrial ribosomal protein MRPS22 leads to Cornelia de Lange-like phenotype, brain abnormalities and hypertrophic cardiomyopathy
Paulien Smits, Ann Saada, Saskia B Wortmann, et al.
Journal of Inherited Metabolic Disease
|
June 19, 2021
Phenotypic diversity, disease progression, and pathogenicity of MVK missense variants in mevalonic aciduria
Heiko Brennenstuhl, Mohammed Nashawi, Julian Schröter, et al.
Journal of Inherited Metabolic Disease
|
October 25, 2025
Palliative Care for Children and Adults With Inherited Metabolic Disease in Europe: An Underutilised Service for Supportive Treatment and Care
Anja Lee, Yngve Thomas Bliksrud, Michela Onali, et al.
Journal of Inherited Metabolic Disease
|
February 2, 2019
Cerebrospinal fluid biogenic amines depletion and brain atrophy in adult patients with phenylketonuria
Andrea Pilotto, Nenad Blau, Edytha Leks, et al.
Journal of Inherited Metabolic Disease
|
April 16, 2026
Real-Life Application of a Point-of-Care Biosensor for Phenylalanine in Patients With Phenylketonuria
Corentin Gondrand, Anna T Reischl-Hajiabadi, Estelle Bonedeau, et al.
Investigative Radiology
|
February 2, 2026
MR Neurography in Children and Adolescents: Multiparametric Assessment of Peripheral Nerve Involvement in Long-chain Fatty Acid Oxidation Disorders
Fabian Preisner, Sven F Garbade, Sarah C Grünert, et al.
Page
of 7
Search research articles
Search
Showing results (41-50 of 63) with videos related to
Sort By:
Page
of 7
Orphanet Journal of Rare Diseases
|
February 29, 2020
Lower plasma cholesterol, LDL-cholesterol and LDL-lipoprotein subclasses in adult phenylketonuria (PKU) patients compared to healthy controls: results of NMR metabolomics investigation
Claire Cannet, Andrea Pilotto, Júlio César Rocha, et al.
Journal of Child Neurology
|
December 29, 2012
Aspartylglucosaminuria: unusual neonatal presentation in Qatari twins with a novel aspartylglucosaminidase gene mutation and 3 new cases in a Turkish family
Thomas Opladen, Friedrich Ebinger, Johannes Zschocke, et al.
Nutrients
|
August 12, 2023
Combined Newborn Screening Allows Comprehensive Identification also of Attenuated Phenotypes for Methylmalonic Acidurias and Homocystinuria
Elena Schnabel, Stefan Kölker, Florian Gleich, et al.
Molecular Genetics and Metabolism
|
February 15, 2025
Kidney involvement in glycogen storage disease type I: Current knowledge and key challenges
Anke Schumann, Sven F Garbade, Skadi Beblo, et al.
European Journal of Human Genetics : EJHG
|
December 30, 2010
Mutation in mitochondrial ribosomal protein MRPS22 leads to Cornelia de Lange-like phenotype, brain abnormalities and hypertrophic cardiomyopathy
Paulien Smits, Ann Saada, Saskia B Wortmann, et al.
Journal of Inherited Metabolic Disease
|
June 19, 2021
Phenotypic diversity, disease progression, and pathogenicity of MVK missense variants in mevalonic aciduria
Heiko Brennenstuhl, Mohammed Nashawi, Julian Schröter, et al.
Journal of Inherited Metabolic Disease
|
October 25, 2025
Palliative Care for Children and Adults With Inherited Metabolic Disease in Europe: An Underutilised Service for Supportive Treatment and Care
Anja Lee, Yngve Thomas Bliksrud, Michela Onali, et al.
Journal of Inherited Metabolic Disease
|
February 2, 2019
Cerebrospinal fluid biogenic amines depletion and brain atrophy in adult patients with phenylketonuria
Andrea Pilotto, Nenad Blau, Edytha Leks, et al.
Journal of Inherited Metabolic Disease
|
April 16, 2026
Real-Life Application of a Point-of-Care Biosensor for Phenylalanine in Patients With Phenylketonuria
Corentin Gondrand, Anna T Reischl-Hajiabadi, Estelle Bonedeau, et al.
Investigative Radiology
|
February 2, 2026
MR Neurography in Children and Adolescents: Multiparametric Assessment of Peripheral Nerve Involvement in Long-chain Fatty Acid Oxidation Disorders
Fabian Preisner, Sven F Garbade, Sarah C Grünert, et al.
Page
of 7