Search research articles
Contact Us
Filters
Showing results (1-10 of 105) with videos related to
Page
of 11
Sort By:
Journal of Inherited Metabolic Disease
|
February 8, 2012
In search of proof-of-concept: gene therapy for glycogen storage disease type Ia
Dwight D Koeberl
Molecular Genetics and Metabolism
|
December 17, 2008
Age-related efficacy with an AAV vector in Fabry disease mice
Dwight D Koeberl
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
June 6, 2006
Vector-related tumorigenesis not found in ornithine transcarbamylase-deficient mice
Dwight D Koeberl
Blood
|
March 7, 2015
A natural choice for hemophilia B
Dwight D Koeberl
The Journal of Clinical Investigation
|
May 17, 2016
Vision of correction for classic homocystinuria
Dwight D Koeberl
Journal of Neurology
|
July 16, 2014
Mitochondrial neurogastrointestinal encephalomyopathy (MNGIE)-like phenotype in a patient with a novel heterozygous POLG mutation
Pankaj Prasun, Dwight D Koeberl
Molecular Therapy. Nucleic Acids
|
February 26, 2026
Seeking stability for gene addition in inborn errors of metabolism
Troy von Beck, Dwight D Koeberl
Journal of Inherited Metabolic Disease
|
September 17, 2014
Large animal models and new therapies for glycogen storage disease
Elizabeth D Brooks, Dwight D Koeberl
Annals of Translational Medicine
|
August 9, 2019
Liver depot gene therapy for Pompe disease
Priya S Kishnani, Dwight D Koeberl
Current Gene Therapy
|
October 8, 2009
Immunomodulatory gene therapy in lysosomal storage disorders
Dwight D Koeberl, Priya S Kishnani
Page
of 11
Search research articles
Search
Showing results (1-10 of 105) with videos related to
Sort By:
Page
of 11
Journal of Inherited Metabolic Disease
|
February 8, 2012
In search of proof-of-concept: gene therapy for glycogen storage disease type Ia
Dwight D Koeberl
Molecular Genetics and Metabolism
|
December 17, 2008
Age-related efficacy with an AAV vector in Fabry disease mice
Dwight D Koeberl
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
June 6, 2006
Vector-related tumorigenesis not found in ornithine transcarbamylase-deficient mice
Dwight D Koeberl
Blood
|
March 7, 2015
A natural choice for hemophilia B
Dwight D Koeberl
The Journal of Clinical Investigation
|
May 17, 2016
Vision of correction for classic homocystinuria
Dwight D Koeberl
Journal of Neurology
|
July 16, 2014
Mitochondrial neurogastrointestinal encephalomyopathy (MNGIE)-like phenotype in a patient with a novel heterozygous POLG mutation
Pankaj Prasun, Dwight D Koeberl
Molecular Therapy. Nucleic Acids
|
February 26, 2026
Seeking stability for gene addition in inborn errors of metabolism
Troy von Beck, Dwight D Koeberl
Journal of Inherited Metabolic Disease
|
September 17, 2014
Large animal models and new therapies for glycogen storage disease
Elizabeth D Brooks, Dwight D Koeberl
Annals of Translational Medicine
|
August 9, 2019
Liver depot gene therapy for Pompe disease
Priya S Kishnani, Dwight D Koeberl
Current Gene Therapy
|
October 8, 2009
Immunomodulatory gene therapy in lysosomal storage disorders
Dwight D Koeberl, Priya S Kishnani
Page
of 11