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Plos One
|
March 28, 2014
Natural history of cone disease in the murine model of Leber congenital amaurosis due to CEP290 mutation: determining the timing and expectation of therapy
Shannon E Boye, Wei-Chieh Huang, Alejandro J Roman, et al.
Plos One
|
May 3, 2013
Targeting photoreceptors via intravitreal delivery using novel, capsid-mutated AAV vectors
Christine N Kay, Renee C Ryals, George V Aslanidi, et al.
Human Gene Therapy
|
August 1, 2012
The human rhodopsin kinase promoter in an AAV5 vector confers rod- and cone-specific expression in the primate retina
Shannon E Boye, John J Alexander, Sanford L Boye, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
April 19, 2020
Novel AAV44.9-Based Vectors Display Exceptional Characteristics for Retinal Gene Therapy
Sanford L Boye, Shreyasi Choudhury, Sean Crosson, et al.
Human Molecular Genetics
|
August 28, 2015
Intravitreal delivery of a novel AAV vector targets ON bipolar cells and restores visual function in a mouse model of complete congenital stationary night blindness
Miranda L Scalabrino, Sanford L Boye, Kathryn M H Fransen, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
April 21, 2011
Virally delivered channelrhodopsin-2 safely and effectively restores visual function in multiple mouse models of blindness
M Mehdi Doroudchi, Kenneth P Greenberg, Jianwen Liu, et al.
Human Gene Therapy. Clinical Development
|
May 23, 2013
Preclinical potency and safety studies of an AAV2-mediated gene therapy vector for the treatment of MERTK associated retinitis pigmentosa
Thomas J Conlon, Wen-Tao Deng, Kirsten Erger, et al.
Human Gene Therapy
|
December 6, 2012
AAV-mediated gene therapy in the guanylate cyclase (RetGC1/RetGC2) double knockout mouse model of Leber congenital amaurosis
Sanford L Boye, Igor V Peshenko, Wei Chieh Huang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
September 29, 2025
A novel multiplex RNAi therapy simultaneously targets Hif1a and Hif2a to defy retinal degeneration in two models of AMD
Lynn J A Ebner, Cornelia Imsand, Duygu Karademir, et al.
Iscience
|
May 17, 2021
Safety and improved efficacy signals following gene therapy in childhood blindness caused by <i>GUCY2D</i> mutations
Samuel G Jacobson, Artur V Cideciyan, Allen C Ho, et al.
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of 19
Search research articles
Search
Showing results (171-180 of 190) with videos related to
Sort By:
Page
of 19
Plos One
|
March 28, 2014
Natural history of cone disease in the murine model of Leber congenital amaurosis due to CEP290 mutation: determining the timing and expectation of therapy
Shannon E Boye, Wei-Chieh Huang, Alejandro J Roman, et al.
Plos One
|
May 3, 2013
Targeting photoreceptors via intravitreal delivery using novel, capsid-mutated AAV vectors
Christine N Kay, Renee C Ryals, George V Aslanidi, et al.
Human Gene Therapy
|
August 1, 2012
The human rhodopsin kinase promoter in an AAV5 vector confers rod- and cone-specific expression in the primate retina
Shannon E Boye, John J Alexander, Sanford L Boye, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
April 19, 2020
Novel AAV44.9-Based Vectors Display Exceptional Characteristics for Retinal Gene Therapy
Sanford L Boye, Shreyasi Choudhury, Sean Crosson, et al.
Human Molecular Genetics
|
August 28, 2015
Intravitreal delivery of a novel AAV vector targets ON bipolar cells and restores visual function in a mouse model of complete congenital stationary night blindness
Miranda L Scalabrino, Sanford L Boye, Kathryn M H Fransen, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
April 21, 2011
Virally delivered channelrhodopsin-2 safely and effectively restores visual function in multiple mouse models of blindness
M Mehdi Doroudchi, Kenneth P Greenberg, Jianwen Liu, et al.
Human Gene Therapy. Clinical Development
|
May 23, 2013
Preclinical potency and safety studies of an AAV2-mediated gene therapy vector for the treatment of MERTK associated retinitis pigmentosa
Thomas J Conlon, Wen-Tao Deng, Kirsten Erger, et al.
Human Gene Therapy
|
December 6, 2012
AAV-mediated gene therapy in the guanylate cyclase (RetGC1/RetGC2) double knockout mouse model of Leber congenital amaurosis
Sanford L Boye, Igor V Peshenko, Wei Chieh Huang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
September 29, 2025
A novel multiplex RNAi therapy simultaneously targets Hif1a and Hif2a to defy retinal degeneration in two models of AMD
Lynn J A Ebner, Cornelia Imsand, Duygu Karademir, et al.
Iscience
|
May 17, 2021
Safety and improved efficacy signals following gene therapy in childhood blindness caused by <i>GUCY2D</i> mutations
Samuel G Jacobson, Artur V Cideciyan, Allen C Ho, et al.
Page
of 19