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The CRISPR Journal|April 2, 2025
Strategies for Interdisciplinary Human Gene Editing Research: Insights from a Swiss ProjectAgnes Kandlbinder, Marie-Hélène Peter-Spiess, Brigitte Leeners, et al.Nature|September 7, 2021
Programmable RNA targeting with the single-protein CRISPR effector Cas7-11Ahsen Özcan, Rohan Krajeski, Eleonora Ioannidi, et al.Science Translational Medicine|March 16, 2022
In vivo prime editing of a metabolic liver disease in miceDesirée Böck, Tanja Rothgangl, Lukas Villiger, et al.Science Translational Medicine|May 13, 2026
Prime editing of a pathogenic Scn1a allele ameliorates seizure phenotypes in a GEFS+ mouse modelLucas Kissling, Francesca Pietrafesa, Matteo Ranucci, et al.Nature Biomedical Engineering|September 19, 2025
Spatial profiling of gene editing by in situ sequencing in mice and macaquesSharan Janjuha, Tatjana Haenggi, Thomas C Chamberlain, et al.Pageof 1