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Stem Cell Reports|November 14, 2025
Advances and challenges in modeling Charcot-Marie-Tooth type 2A using iPSC-derived modelsMafalda Rizzuti, Elisa Pagliari, Martina D'Agostino, et al.Biomedicines|March 25, 2022
Stathmins and Motor Neuron Diseases: Pathophysiology and Therapeutic TargetsDelia Gagliardi, Elisa Pagliari, Megi Meneri, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|November 22, 2021
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical modelMargherita Bersani, Mafalda Rizzuti, Elisa Pagliari, et al.Cellular and Molecular Life Sciences : CMLS|December 26, 2024
Targeting STMN2 for neuroprotection and neuromuscular recovery in Spinal Muscular Atrophy: evidence from in vitro and in vivo SMA modelsElisa Pagliari, Michela Taiana, Paolo Manzini, et al.Journal of Biomedical Science|January 4, 2026
AAV9 gene therapy optimization for SMARD1/CMT2S: safety and long-term efficacy comparison of two vectors in a SMARD1 preclinical modelElisa Pagliari, Alessia Anastasia, Floriana Bellandi, et al.Proceedings of the National Academy of Sciences of the United States of America|May 1, 2021
Impairment of the neurotrophic signaling hub B-Raf contributes to motoneuron degeneration in spinal muscular atrophyNiko Hensel, Federica Cieri, Pamela Santonicola, et al.Pageof 1