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Thescientificworldjournal
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December 3, 2013
Medium-chain acyl-CoA deficiency: outlines from newborn screening, in silico predictions, and molecular studies
Serena Catarzi, Anna Caciotti, Janita Thusberg, et al.
Orphanet Journal of Rare Diseases
|
July 17, 2014
Sudden unexpected fatal encephalopathy in adults with OTC gene mutations-Clues for early diagnosis and timely treatment
Catia Cavicchi, Maria Donati, Rossella Parini, et al.
Laboratory Investigation; a Journal of Technical Methods and Pathology
|
February 7, 2008
Caveolin-3 T78M and T78K missense mutations lead to different phenotypes in vivo and in vitro
Monica Traverso, Elisabetta Gazzerro, Stefania Assereto, et al.
BBA Clinical
|
April 7, 2016
Clinical relevance of short-chain acyl-CoA dehydrogenase (SCAD) deficiency: Exploring the role of new variants including the first SCAD-disease-causing allele carrying a synonymous mutation
Rodolfo Tonin, Anna Caciotti, Silvia Funghini, et al.
JIMD Reports
|
April 18, 2014
Common and Novel TMEM70 Mutations in a Cohort of Italian Patients with Mitochondrial Encephalocardiomyopathy
Daria Diodato, Federica Invernizzi, Eleonora Lamantea, et al.
Orphanet Journal of Rare Diseases
|
May 31, 2012
3-methylcrotonyl-CoA carboxylase deficiency: clinical, biochemical, enzymatic and molecular studies in 88 individuals
Sarah C Grünert, Martin Stucki, Raphael J Morscher, et al.
Journal of Inherited Metabolic Disease
|
February 17, 2022
3-Hydroxyisobutyric acid dehydrogenase deficiency: Expanding the clinical spectrum and quantitation of D- and L-3-Hydroxyisobutyric acid by an LC-MS/MS method
Florin Sasarman, Sacha Ferdinandusse, David S Sinasac, et al.
Journal of Inherited Metabolic Disease
|
December 2, 2016
Guidelines for diagnosis and management of the cobalamin-related remethylation disorders cblC, cblD, cblE, cblF, cblG, cblJ and MTHFR deficiency
Martina Huemer, Daria Diodato, Bernd Schwahn, et al.
Ebiomedicine
|
March 30, 2019
A genetic modifier of symptom onset in Pompe disease
Atze J Bergsma, Stijn L M In 't Groen, Jan J A van den Dorpel, et al.
Neuromuscular Disorders : NMD
|
July 17, 2010
North Star Ambulatory Assessment, 6-minute walk test and timed items in ambulant boys with Duchenne muscular dystrophy
Elena Mazzone, Diego Martinelli, Angela Berardinelli, et al.
Page
of 4
Search research articles
Search
Showing results (21-30 of 33) with videos related to
Sort By:
Page
of 4
Thescientificworldjournal
|
December 3, 2013
Medium-chain acyl-CoA deficiency: outlines from newborn screening, in silico predictions, and molecular studies
Serena Catarzi, Anna Caciotti, Janita Thusberg, et al.
Orphanet Journal of Rare Diseases
|
July 17, 2014
Sudden unexpected fatal encephalopathy in adults with OTC gene mutations-Clues for early diagnosis and timely treatment
Catia Cavicchi, Maria Donati, Rossella Parini, et al.
Laboratory Investigation; a Journal of Technical Methods and Pathology
|
February 7, 2008
Caveolin-3 T78M and T78K missense mutations lead to different phenotypes in vivo and in vitro
Monica Traverso, Elisabetta Gazzerro, Stefania Assereto, et al.
BBA Clinical
|
April 7, 2016
Clinical relevance of short-chain acyl-CoA dehydrogenase (SCAD) deficiency: Exploring the role of new variants including the first SCAD-disease-causing allele carrying a synonymous mutation
Rodolfo Tonin, Anna Caciotti, Silvia Funghini, et al.
JIMD Reports
|
April 18, 2014
Common and Novel TMEM70 Mutations in a Cohort of Italian Patients with Mitochondrial Encephalocardiomyopathy
Daria Diodato, Federica Invernizzi, Eleonora Lamantea, et al.
Orphanet Journal of Rare Diseases
|
May 31, 2012
3-methylcrotonyl-CoA carboxylase deficiency: clinical, biochemical, enzymatic and molecular studies in 88 individuals
Sarah C Grünert, Martin Stucki, Raphael J Morscher, et al.
Journal of Inherited Metabolic Disease
|
February 17, 2022
3-Hydroxyisobutyric acid dehydrogenase deficiency: Expanding the clinical spectrum and quantitation of D- and L-3-Hydroxyisobutyric acid by an LC-MS/MS method
Florin Sasarman, Sacha Ferdinandusse, David S Sinasac, et al.
Journal of Inherited Metabolic Disease
|
December 2, 2016
Guidelines for diagnosis and management of the cobalamin-related remethylation disorders cblC, cblD, cblE, cblF, cblG, cblJ and MTHFR deficiency
Martina Huemer, Daria Diodato, Bernd Schwahn, et al.
Ebiomedicine
|
March 30, 2019
A genetic modifier of symptom onset in Pompe disease
Atze J Bergsma, Stijn L M In 't Groen, Jan J A van den Dorpel, et al.
Neuromuscular Disorders : NMD
|
July 17, 2010
North Star Ambulatory Assessment, 6-minute walk test and timed items in ambulant boys with Duchenne muscular dystrophy
Elena Mazzone, Diego Martinelli, Angela Berardinelli, et al.
Page
of 4