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Human Molecular Genetics
|
November 1, 2017
Abnormal creatine transport of mutations in monocarboxylate transporter 12 (MCT12) found in patients with age-related cataract can be partially rescued by exogenous chaperone CD147
Andrina Stäubli, Nadejda Capatina, Yvonne Fuhrer, et al.
Blood
|
January 8, 2017
Biallelic mutations in <i>DNAJC21</i> cause Shwachman-Diamond syndrome
Santhosh Dhanraj, Anna Matveev, Hongbing Li, et al.
Investigative Ophthalmology & Visual Science
|
December 22, 2023
Treatment Strategy With Gene Editing for Late-Onset Retinal Degeneration Caused by a Founder Variant in C1QTNF5
Randa T H Li, Alejandro J Roman, Alexander Sumaroka, et al.
Human Molecular Genetics
|
October 5, 2012
Determining consequences of retinal membrane guanylyl cyclase (RetGC1) deficiency in human Leber congenital amaurosis en route to therapy: residual cone-photoreceptor vision correlates with biochemical properties of the mutants
Samuel G Jacobson, Artur V Cideciyan, Igor V Peshenko, et al.
NPJ Genomic Medicine
|
March 28, 2026
A novel phenotype-guided genome analysis pipeline for variant discovery
Layla Ahmed, Erika Tavares, Janice Min Li, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
April 20, 2005
Identifying photoreceptors in blind eyes caused by RPE65 mutations: Prerequisite for human gene therapy success
Samuel G Jacobson, Tomas S Aleman, Artur V Cideciyan, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
September 13, 2007
Human cone photoreceptor dependence on RPE65 isomerase
Samuel G Jacobson, Tomas S Aleman, Artur V Cideciyan, et al.
Journal of AAPOS : the Official Publication of the American Association for Pediatric Ophthalmology and Strabismus
|
June 25, 2019
Survey of practice patterns for the management of ophthalmic genetic disorders among AAPOS members: report by the AAPOS Genetic Eye Disease Task Force
Arlene V Drack, Virginia Miraldi Utz, Kai Wang, et al.
American Journal of Ophthalmology
|
December 22, 2023
Functional Vision in Patients With Biallelic USH2A Variants
Elise Heon, Michele Melia, Laura E Bocchino, et al.
Clinical Genetics
|
August 2, 2022
Deep intronic variant in MVK as a cause for mevalonic aciduria initially presenting as non-syndromic retinitis pigmentosa
Anna Dvaladze, Erika Tavares, Matteo Di Scipio, et al.
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of 9
Search research articles
Search
Showing results (51-60 of 87) with videos related to
Sort By:
Page
of 9
Human Molecular Genetics
|
November 1, 2017
Abnormal creatine transport of mutations in monocarboxylate transporter 12 (MCT12) found in patients with age-related cataract can be partially rescued by exogenous chaperone CD147
Andrina Stäubli, Nadejda Capatina, Yvonne Fuhrer, et al.
Blood
|
January 8, 2017
Biallelic mutations in <i>DNAJC21</i> cause Shwachman-Diamond syndrome
Santhosh Dhanraj, Anna Matveev, Hongbing Li, et al.
Investigative Ophthalmology & Visual Science
|
December 22, 2023
Treatment Strategy With Gene Editing for Late-Onset Retinal Degeneration Caused by a Founder Variant in C1QTNF5
Randa T H Li, Alejandro J Roman, Alexander Sumaroka, et al.
Human Molecular Genetics
|
October 5, 2012
Determining consequences of retinal membrane guanylyl cyclase (RetGC1) deficiency in human Leber congenital amaurosis en route to therapy: residual cone-photoreceptor vision correlates with biochemical properties of the mutants
Samuel G Jacobson, Artur V Cideciyan, Igor V Peshenko, et al.
NPJ Genomic Medicine
|
March 28, 2026
A novel phenotype-guided genome analysis pipeline for variant discovery
Layla Ahmed, Erika Tavares, Janice Min Li, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
April 20, 2005
Identifying photoreceptors in blind eyes caused by RPE65 mutations: Prerequisite for human gene therapy success
Samuel G Jacobson, Tomas S Aleman, Artur V Cideciyan, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
September 13, 2007
Human cone photoreceptor dependence on RPE65 isomerase
Samuel G Jacobson, Tomas S Aleman, Artur V Cideciyan, et al.
Journal of AAPOS : the Official Publication of the American Association for Pediatric Ophthalmology and Strabismus
|
June 25, 2019
Survey of practice patterns for the management of ophthalmic genetic disorders among AAPOS members: report by the AAPOS Genetic Eye Disease Task Force
Arlene V Drack, Virginia Miraldi Utz, Kai Wang, et al.
American Journal of Ophthalmology
|
December 22, 2023
Functional Vision in Patients With Biallelic USH2A Variants
Elise Heon, Michele Melia, Laura E Bocchino, et al.
Clinical Genetics
|
August 2, 2022
Deep intronic variant in MVK as a cause for mevalonic aciduria initially presenting as non-syndromic retinitis pigmentosa
Anna Dvaladze, Erika Tavares, Matteo Di Scipio, et al.
Page
of 9