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Journal of Neurodevelopmental Disorders
|
April 4, 2020
Correction to: Expressive language sampling as a source of outcome measures for treatment studies in fragile X syndrome: feasibility, practice effects, test-retest reliability, and construct validity
Leonard Abbeduto, Elizabeth Berry-Kravis, Audra Sterling, et al.
Genes
|
September 23, 2022
Observable Symptoms of Anxiety in Individuals with Fragile X Syndrome: Parent and Caregiver Perspectives
Reymundo Lozano, Talia Thompson, Jayne Dixon-Weber, et al.
Pediatric Neurology
|
November 26, 2022
DDX3X Syndrome: Summary of Findings and Recommendations for Evaluation and Care
Tess Levy, Paige M Siper, Bonnie Lerman, et al.
The Biochemical Journal
|
June 2, 2010
Evidence of mitochondrial dysfunction in fragile X-associated tremor/ataxia syndrome
Catherine Ross-Inta, Alicja Omanska-Klusek, Sarah Wong, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
December 5, 2022
Neurofilament light chain in cerebrospinal fluid as a novel biomarker in evaluating both clinical severity and therapeutic response in Niemann-Pick disease type C1
Neena Agrawal, Nicole Y Farhat, Ninet Sinaii, et al.
The Journal of Molecular Diagnostics : JMD
|
May 18, 2013
Development of a genomic DNA reference material panel for myotonic dystrophy type 1 (DM1) genetic testing
Lisa Kalman, Jack Tarleton, Monica Hitch, et al.
Plos One
|
March 12, 2010
Array-based FMR1 sequencing and deletion analysis in patients with a fragile X syndrome-like phenotype
Stephen C Collins, Brad Coffee, Paul J Benke, et al.
Molecular Genetics and Metabolism
|
November 19, 2025
Utility of 24(S)-hydroxycholesterol as a proximal biomarker to monitor long-term intrathecal adrabetadex therapy in individuals with Niemann-Pick disease, type C1
Forbes D Porter, Derek M Alexander, Orsolya K Albert, et al.
Cerebellum (London, England)
|
July 4, 2016
Clinical Phenotype of Adult Fragile X Gray Zone Allele Carriers: a Case Series
Sarah M Debrey, Maureen A Leehey, Olga Klepitskaya, et al.
Pediatric Neurology
|
February 13, 2018
Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-β-Cyclodextrin
Elizabeth Berry-Kravis, Jamie Chin, Anne Hoffmann, et al.
Page
of 27
Search research articles
Search
Showing results (141-150 of 265) with videos related to
Sort By:
Page
of 27
Journal of Neurodevelopmental Disorders
|
April 4, 2020
Correction to: Expressive language sampling as a source of outcome measures for treatment studies in fragile X syndrome: feasibility, practice effects, test-retest reliability, and construct validity
Leonard Abbeduto, Elizabeth Berry-Kravis, Audra Sterling, et al.
Genes
|
September 23, 2022
Observable Symptoms of Anxiety in Individuals with Fragile X Syndrome: Parent and Caregiver Perspectives
Reymundo Lozano, Talia Thompson, Jayne Dixon-Weber, et al.
Pediatric Neurology
|
November 26, 2022
DDX3X Syndrome: Summary of Findings and Recommendations for Evaluation and Care
Tess Levy, Paige M Siper, Bonnie Lerman, et al.
The Biochemical Journal
|
June 2, 2010
Evidence of mitochondrial dysfunction in fragile X-associated tremor/ataxia syndrome
Catherine Ross-Inta, Alicja Omanska-Klusek, Sarah Wong, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
December 5, 2022
Neurofilament light chain in cerebrospinal fluid as a novel biomarker in evaluating both clinical severity and therapeutic response in Niemann-Pick disease type C1
Neena Agrawal, Nicole Y Farhat, Ninet Sinaii, et al.
The Journal of Molecular Diagnostics : JMD
|
May 18, 2013
Development of a genomic DNA reference material panel for myotonic dystrophy type 1 (DM1) genetic testing
Lisa Kalman, Jack Tarleton, Monica Hitch, et al.
Plos One
|
March 12, 2010
Array-based FMR1 sequencing and deletion analysis in patients with a fragile X syndrome-like phenotype
Stephen C Collins, Brad Coffee, Paul J Benke, et al.
Molecular Genetics and Metabolism
|
November 19, 2025
Utility of 24(S)-hydroxycholesterol as a proximal biomarker to monitor long-term intrathecal adrabetadex therapy in individuals with Niemann-Pick disease, type C1
Forbes D Porter, Derek M Alexander, Orsolya K Albert, et al.
Cerebellum (London, England)
|
July 4, 2016
Clinical Phenotype of Adult Fragile X Gray Zone Allele Carriers: a Case Series
Sarah M Debrey, Maureen A Leehey, Olga Klepitskaya, et al.
Pediatric Neurology
|
February 13, 2018
Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-β-Cyclodextrin
Elizabeth Berry-Kravis, Jamie Chin, Anne Hoffmann, et al.
Page
of 27