Search research articles
Contact Us
Filters
Showing results (51-60 of 66) with videos related to
Page
of 7
Sort By:
Journal of Medical Genetics
|
April 20, 2016
A recurrent mitochondrial p.Trp22Arg NDUFB3 variant causes a distinctive facial appearance, short stature and a mild biochemical and clinical phenotype
Charlotte L Alston, Caoimhe Howard, Monika Oláhová, et al.
Orphanet Journal of Rare Diseases
|
April 8, 2018
Consensus clinical management guidelines for Niemann-Pick disease type C
Tarekegn Geberhiwot, Alessandro Moro, Andrea Dardis, et al.
Journal of Medical Genetics
|
January 24, 2018
Catalogue of inherited disorders found among the Irish Traveller population
Sally Ann Lynch, Ellen Crushell, Deborah M Lambert, et al.
Archives of Disease in Childhood
|
May 5, 2017
Diagnosing childhood-onset inborn errors of metabolism by next-generation sequencing
Arunabha Ghosh, Helene Schlecht, Lesley E Heptinstall, et al.
Journal of Inherited Metabolic Disease
|
October 26, 2016
Guidelines for the diagnosis and management of cystathionine beta-synthase deficiency
Andrew A M Morris, Viktor Kožich, Saikat Santra, et al.
Molecular Genetics and Metabolism
|
May 11, 2024
Empagliflozin for treating neutropenia and neutrophil dysfunction in 21 infants with glycogen storage disease 1b
Sarah C Grünert, Matthias Gautschi, Joshua Baker, et al.
Liver International : Official Journal of the International Association for the Study of the Liver
|
May 28, 2025
Hepatic Phenotype in NBAS-Associated Disease: Clinical Course, Prognostic Factors and Outcome in 230 Patients
Bianca Peters, Lea Dewi Schlieben, Heiko Brennenstuhl, et al.
Molecular Genetics and Metabolism
|
January 20, 2024
Impact of genetic and non-genetic factors on phenotypic diversity in NBAS-associated disease
Nicole Hammann, Dominic Lenz, Ivo Baric, et al.
Nature Communications
|
May 28, 2016
ATP6AP1 deficiency causes an immunodeficiency with hepatopathy, cognitive impairment and abnormal protein glycosylation
Eric J R Jansen, Sharita Timal, Margret Ryan, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 24, 2020
Genotypic diversity and phenotypic spectrum of infantile liver failure syndrome type 1 due to variants in LARS1
Dominic Lenz, Desirée E C Smith, Ellen Crushell, et al.
Page
of 7
Search research articles
Search
Showing results (51-60 of 66) with videos related to
Sort By:
Page
of 7
Journal of Medical Genetics
|
April 20, 2016
A recurrent mitochondrial p.Trp22Arg NDUFB3 variant causes a distinctive facial appearance, short stature and a mild biochemical and clinical phenotype
Charlotte L Alston, Caoimhe Howard, Monika Oláhová, et al.
Orphanet Journal of Rare Diseases
|
April 8, 2018
Consensus clinical management guidelines for Niemann-Pick disease type C
Tarekegn Geberhiwot, Alessandro Moro, Andrea Dardis, et al.
Journal of Medical Genetics
|
January 24, 2018
Catalogue of inherited disorders found among the Irish Traveller population
Sally Ann Lynch, Ellen Crushell, Deborah M Lambert, et al.
Archives of Disease in Childhood
|
May 5, 2017
Diagnosing childhood-onset inborn errors of metabolism by next-generation sequencing
Arunabha Ghosh, Helene Schlecht, Lesley E Heptinstall, et al.
Journal of Inherited Metabolic Disease
|
October 26, 2016
Guidelines for the diagnosis and management of cystathionine beta-synthase deficiency
Andrew A M Morris, Viktor Kožich, Saikat Santra, et al.
Molecular Genetics and Metabolism
|
May 11, 2024
Empagliflozin for treating neutropenia and neutrophil dysfunction in 21 infants with glycogen storage disease 1b
Sarah C Grünert, Matthias Gautschi, Joshua Baker, et al.
Liver International : Official Journal of the International Association for the Study of the Liver
|
May 28, 2025
Hepatic Phenotype in NBAS-Associated Disease: Clinical Course, Prognostic Factors and Outcome in 230 Patients
Bianca Peters, Lea Dewi Schlieben, Heiko Brennenstuhl, et al.
Molecular Genetics and Metabolism
|
January 20, 2024
Impact of genetic and non-genetic factors on phenotypic diversity in NBAS-associated disease
Nicole Hammann, Dominic Lenz, Ivo Baric, et al.
Nature Communications
|
May 28, 2016
ATP6AP1 deficiency causes an immunodeficiency with hepatopathy, cognitive impairment and abnormal protein glycosylation
Eric J R Jansen, Sharita Timal, Margret Ryan, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
July 24, 2020
Genotypic diversity and phenotypic spectrum of infantile liver failure syndrome type 1 due to variants in LARS1
Dominic Lenz, Desirée E C Smith, Ellen Crushell, et al.
Page
of 7