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Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 3, 2021
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia
Tiwaporn Nualkaew, Karine Sii-Felice, Marie Giorgi, et al.
Stem Cells (Dayton, Ohio)
|
May 29, 2013
Parallel assessment of globin lentiviral transfer in induced pluripotent stem cells and adult hematopoietic stem cells derived from the same transplanted β-thalassemia patient
Alisa Tubsuwan, Soumeya Abed, Annette Deichmann, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 10, 2017
Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies
Kanit Bhukhai, Edouard de Dreuzy, Marie Giorgi, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
October 23, 2002
Permanent and panerythroid correction of murine beta thalassemia by multiple lentiviral integration in hematopoietic stem cells
Suzan Imren, Emmanuel Payen, Karen A Westerman, et al.
Molecular Therapy. Methods & Clinical Development
|
November 4, 2015
Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles
Anne Prel, Vincent Caval, Régis Gayon, et al.
Haematologica
|
June 20, 2015
Transplantation of Macaca cynomolgus iPS-derived hematopoietic cells in NSG immunodeficient mice
Soumeya Abed, Alisa Tubsuwan, Porntip Chaichompoo, et al.
Nature Medicine
|
March 25, 2014
An activin receptor IIA ligand trap corrects ineffective erythropoiesis in β-thalassemia
Michael Dussiot, Thiago T Maciel, Aurélie Fricot, et al.
Current Gene Therapy
|
November 28, 2014
Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease
Olivier Negre, Cynthia Bartholomae, Yves Beuzard, et al.
Science (New York, N.Y.)
|
November 7, 2009
Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy
Nathalie Cartier, Salima Hacein-Bey-Abina, Cynthia C Bartholomae, et al.
The New England Journal of Medicine
|
March 2, 2017
Gene Therapy in a Patient with Sickle Cell Disease
Jean-Antoine Ribeil, Salima Hacein-Bey-Abina, Emmanuel Payen, et al.
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Search research articles
Search
Showing results (21-30 of 33) with videos related to
Sort By:
Page
of 4
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 3, 2021
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia
Tiwaporn Nualkaew, Karine Sii-Felice, Marie Giorgi, et al.
Stem Cells (Dayton, Ohio)
|
May 29, 2013
Parallel assessment of globin lentiviral transfer in induced pluripotent stem cells and adult hematopoietic stem cells derived from the same transplanted β-thalassemia patient
Alisa Tubsuwan, Soumeya Abed, Annette Deichmann, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 10, 2017
Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies
Kanit Bhukhai, Edouard de Dreuzy, Marie Giorgi, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
October 23, 2002
Permanent and panerythroid correction of murine beta thalassemia by multiple lentiviral integration in hematopoietic stem cells
Suzan Imren, Emmanuel Payen, Karen A Westerman, et al.
Molecular Therapy. Methods & Clinical Development
|
November 4, 2015
Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles
Anne Prel, Vincent Caval, Régis Gayon, et al.
Haematologica
|
June 20, 2015
Transplantation of Macaca cynomolgus iPS-derived hematopoietic cells in NSG immunodeficient mice
Soumeya Abed, Alisa Tubsuwan, Porntip Chaichompoo, et al.
Nature Medicine
|
March 25, 2014
An activin receptor IIA ligand trap corrects ineffective erythropoiesis in β-thalassemia
Michael Dussiot, Thiago T Maciel, Aurélie Fricot, et al.
Current Gene Therapy
|
November 28, 2014
Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease
Olivier Negre, Cynthia Bartholomae, Yves Beuzard, et al.
Science (New York, N.Y.)
|
November 7, 2009
Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy
Nathalie Cartier, Salima Hacein-Bey-Abina, Cynthia C Bartholomae, et al.
The New England Journal of Medicine
|
March 2, 2017
Gene Therapy in a Patient with Sickle Cell Disease
Jean-Antoine Ribeil, Salima Hacein-Bey-Abina, Emmanuel Payen, et al.
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of 4