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Human Molecular Genetics
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August 30, 2014
Mutations in IFT172 cause isolated retinal degeneration and Bardet-Biedl syndrome
Kinga M Bujakowska, Qi Zhang, Anna M Siemiatkowska, et al.
American Journal of Human Genetics
|
May 5, 2009
Loss of the metalloprotease ADAM9 leads to cone-rod dystrophy in humans and retinal degeneration in mice
David A Parry, Carmel Toomes, Lina Bida, et al.
NPJ Genomic Medicine
|
June 30, 2021
Broadening INPP5E phenotypic spectrum: detection of rare variants in syndromic and non-syndromic IRD
Riccardo Sangermano, Iris Deitch, Virginie G Peter, et al.
American Journal of Human Genetics
|
May 11, 2020
Mutations in the Kinesin-2 Motor KIF3B Cause an Autosomal-Dominant Ciliopathy
Benjamin Cogné, Xenia Latypova, Lokuliyanage Dona Samudita Senaratne, et al.
Nature Genetics
|
July 31, 2012
NMNAT1 mutations cause Leber congenital amaurosis
Marni J Falk, Qi Zhang, Eiko Nakamaru-Ogiso, et al.
The New England Journal of Medicine
|
April 29, 2008
Safety and efficacy of gene transfer for Leber's congenital amaurosis
Albert M Maguire, Francesca Simonelli, Eric A Pierce, et al.
Lancet (London, England)
|
October 27, 2009
Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial
Albert M Maguire, Katherine A High, Alberto Auricchio, et al.
Medrxiv : the Preprint Server for Health Sciences
|
January 7, 2025
Mitochondrial DNA variant detection in over 6,500 rare disease families by the systematic analysis of exome and genome sequencing data resolves undiagnosed cases
Sarah L Stenton, Kristen Laricchia, Nicole J Lake, et al.
HGG Advances
|
April 17, 2025
Mitochondrial DNA variant detection in over 6,500 rare disease families by the systematic analysis of exome and genome sequencing data resolves undiagnosed cases
Sarah L Stenton, Kristen Laricchia, Nicole J Lake, et al.
Translational Vision Science & Technology
|
August 25, 2020
Advancing Clinical Trials for Inherited Retinal Diseases: Recommendations from the Second Monaciano Symposium
Debra A Thompson, Alessandro Iannaccone, Robin R Ali, et al.
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of 14
Search research articles
Search
Showing results (111-120 of 132) with videos related to
Sort By:
Page
of 14
Human Molecular Genetics
|
August 30, 2014
Mutations in IFT172 cause isolated retinal degeneration and Bardet-Biedl syndrome
Kinga M Bujakowska, Qi Zhang, Anna M Siemiatkowska, et al.
American Journal of Human Genetics
|
May 5, 2009
Loss of the metalloprotease ADAM9 leads to cone-rod dystrophy in humans and retinal degeneration in mice
David A Parry, Carmel Toomes, Lina Bida, et al.
NPJ Genomic Medicine
|
June 30, 2021
Broadening INPP5E phenotypic spectrum: detection of rare variants in syndromic and non-syndromic IRD
Riccardo Sangermano, Iris Deitch, Virginie G Peter, et al.
American Journal of Human Genetics
|
May 11, 2020
Mutations in the Kinesin-2 Motor KIF3B Cause an Autosomal-Dominant Ciliopathy
Benjamin Cogné, Xenia Latypova, Lokuliyanage Dona Samudita Senaratne, et al.
Nature Genetics
|
July 31, 2012
NMNAT1 mutations cause Leber congenital amaurosis
Marni J Falk, Qi Zhang, Eiko Nakamaru-Ogiso, et al.
The New England Journal of Medicine
|
April 29, 2008
Safety and efficacy of gene transfer for Leber's congenital amaurosis
Albert M Maguire, Francesca Simonelli, Eric A Pierce, et al.
Lancet (London, England)
|
October 27, 2009
Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial
Albert M Maguire, Katherine A High, Alberto Auricchio, et al.
Medrxiv : the Preprint Server for Health Sciences
|
January 7, 2025
Mitochondrial DNA variant detection in over 6,500 rare disease families by the systematic analysis of exome and genome sequencing data resolves undiagnosed cases
Sarah L Stenton, Kristen Laricchia, Nicole J Lake, et al.
HGG Advances
|
April 17, 2025
Mitochondrial DNA variant detection in over 6,500 rare disease families by the systematic analysis of exome and genome sequencing data resolves undiagnosed cases
Sarah L Stenton, Kristen Laricchia, Nicole J Lake, et al.
Translational Vision Science & Technology
|
August 25, 2020
Advancing Clinical Trials for Inherited Retinal Diseases: Recommendations from the Second Monaciano Symposium
Debra A Thompson, Alessandro Iannaccone, Robin R Ali, et al.
Page
of 14