Search research articles
Contact Us
Filters
Showing results (81-90 of 88) with videos related to
Page
of 9
Sort By:
You have reached the last page of results.
This site can display upto 88 results.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 21, 2026
Enhanced antisense oligonucleotide delivery reveals that transcript turnover impacts apparent splicing rescue in myotonic dystrophy
Emma N Shea, Hailey R Olafson, Derek R Muscato, et al.
The Journal of Clinical Endocrinology and Metabolism
|
September 10, 2010
Molecular classification of thyroid nodules using high-dimensionality genomic data
Darya Chudova, Jonathan I Wilde, Eric T Wang, et al.
Brain : a Journal of Neurology
|
May 5, 2023
Choroid plexus mis-splicing and altered cerebrospinal fluid composition in myotonic dystrophy type 1
Curtis A Nutter, Benjamin M Kidd, Helmut A Carter, et al.
Scientific Reports
|
August 24, 2021
High-content image-based analysis and proteomic profiling identifies Tau phosphorylation inhibitors in a human iPSC-derived glutamatergic neuronal model of tauopathy
Chialin Cheng, Surya A Reis, Emily T Adams, et al.
ACS Chemical Biology
|
February 20, 2026
Modified Polycyclic Compounds Rescue Mis-splicing in Myotonic Dystrophy Type 1 Disease Models
Jesus A Frias, Sawyer M Hicks, Hormoz Mazdiyasni, et al.
Biorxiv : the Preprint Server for Biology
|
May 7, 2025
Interventionally targeting somatic CAG expansions can be a rapid disease-modifying therapeutic avenue: Preclinical evidence
Terence Gall-Duncan, Sangyoon Y Ko, Isabelle K Quick, et al.
Science Translational Medicine
|
October 27, 2021
Ribonuclease recruitment using a small molecule reduced c9ALS/FTD r(G<sub>4</sub>C<sub>2</sub>) repeat expansion in vitro and in vivo ALS models
Jessica A Bush, Haruo Aikawa, Rita Fuerst, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
February 12, 2025
<i>CASP8</i> intronic expansion identified by poly-glycine-arginine pathology increases Alzheimer's disease risk
Lien Nguyen, Ramadan Ajredini, Shu Guo, et al.
Page
of 9
Search research articles
Search
Showing results (81-90 of 88) with videos related to
Sort By:
Page
of 9
You have reached the last page of results.
This site can display upto 88 results.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 21, 2026
Enhanced antisense oligonucleotide delivery reveals that transcript turnover impacts apparent splicing rescue in myotonic dystrophy
Emma N Shea, Hailey R Olafson, Derek R Muscato, et al.
The Journal of Clinical Endocrinology and Metabolism
|
September 10, 2010
Molecular classification of thyroid nodules using high-dimensionality genomic data
Darya Chudova, Jonathan I Wilde, Eric T Wang, et al.
Brain : a Journal of Neurology
|
May 5, 2023
Choroid plexus mis-splicing and altered cerebrospinal fluid composition in myotonic dystrophy type 1
Curtis A Nutter, Benjamin M Kidd, Helmut A Carter, et al.
Scientific Reports
|
August 24, 2021
High-content image-based analysis and proteomic profiling identifies Tau phosphorylation inhibitors in a human iPSC-derived glutamatergic neuronal model of tauopathy
Chialin Cheng, Surya A Reis, Emily T Adams, et al.
ACS Chemical Biology
|
February 20, 2026
Modified Polycyclic Compounds Rescue Mis-splicing in Myotonic Dystrophy Type 1 Disease Models
Jesus A Frias, Sawyer M Hicks, Hormoz Mazdiyasni, et al.
Biorxiv : the Preprint Server for Biology
|
May 7, 2025
Interventionally targeting somatic CAG expansions can be a rapid disease-modifying therapeutic avenue: Preclinical evidence
Terence Gall-Duncan, Sangyoon Y Ko, Isabelle K Quick, et al.
Science Translational Medicine
|
October 27, 2021
Ribonuclease recruitment using a small molecule reduced c9ALS/FTD r(G<sub>4</sub>C<sub>2</sub>) repeat expansion in vitro and in vivo ALS models
Jessica A Bush, Haruo Aikawa, Rita Fuerst, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
February 12, 2025
<i>CASP8</i> intronic expansion identified by poly-glycine-arginine pathology increases Alzheimer's disease risk
Lien Nguyen, Ramadan Ajredini, Shu Guo, et al.
Page
of 9