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American Journal of Medical Genetics. Part A
|
October 24, 2020
Growth hormone deficiency in a child with branchio-oto-renal spectrum disorder: Clinical evidence of EYA1 in pituitary development and a recommendation for pituitary function surveillance
Karthik Muthusamy, Christian Hanna, Derek R Johnson, et al.
American Journal of Medical Genetics. Part A
|
March 14, 2012
De Barsy Syndrome: a genetically heterogeneous autosomal recessive cutis laxa syndrome related to P5CS and PYCR1 dysfunction
Stefania Zampatti, Marco Castori, Bjoern Fischer, et al.
European Journal of Medical Genetics
|
October 29, 2017
Congenital disorders of glycosylation (CDG): Quo vadis?
Romain Péanne, Pascale de Lonlay, François Foulquier, et al.
Clinical Chemistry
|
November 25, 2003
N-acetylated metabolites in urine: proton nuclear magnetic resonance spectroscopic study on patients with inborn errors of metabolism
Udo F H Engelke, Maria L F Liebrand-van Sambeek, Jan G N de Jong, et al.
Clinical Chemistry
|
October 28, 2003
Apolipoprotein C-III isofocusing in the diagnosis of genetic defects in O-glycan biosynthesis
Suzan Wopereis, Stephanie Grünewald, Eva Morava, et al.
Molecular Genetics and Metabolism
|
November 10, 2016
Autism in patients with propionic acidemia
Peter Witters, Eric Debbold, Kea Crivelly, et al.
Molecular Genetics and Metabolism
|
June 25, 2024
Cardiomyopathy, an uncommon phenotype of congenital disorders of glycosylation: Recommendations for baseline screening and follow-up evaluation
Roni Zemet, Kyle D Hope, Andrew C Edmondson, et al.
European Journal of Human Genetics : EJHG
|
October 8, 2009
Functional consequences of mitochondrial tRNA Trp and tRNA Arg mutations causing combined OXPHOS defects
Paulien Smits, Sandy Mattijssen, Eva Morava, et al.
Journal of Inherited Metabolic Disease
|
October 19, 2014
TMEM70 deficiency: long-term outcome of 48 patients
Martin Magner, Veronika Dvorakova, Marketa Tesarova, et al.
Molecular Genetics and Metabolism
|
May 24, 2023
Coagulation abnormalities in a prospective cohort of 50 patients with PMM2-congenital disorder of glycosylation
Diederik De Graef, Anna N Ligezka, Joseph Rezents, et al.
Page
of 36
Search research articles
Search
Showing results (211-220 of 355) with videos related to
Sort By:
Page
of 36
American Journal of Medical Genetics. Part A
|
October 24, 2020
Growth hormone deficiency in a child with branchio-oto-renal spectrum disorder: Clinical evidence of EYA1 in pituitary development and a recommendation for pituitary function surveillance
Karthik Muthusamy, Christian Hanna, Derek R Johnson, et al.
American Journal of Medical Genetics. Part A
|
March 14, 2012
De Barsy Syndrome: a genetically heterogeneous autosomal recessive cutis laxa syndrome related to P5CS and PYCR1 dysfunction
Stefania Zampatti, Marco Castori, Bjoern Fischer, et al.
European Journal of Medical Genetics
|
October 29, 2017
Congenital disorders of glycosylation (CDG): Quo vadis?
Romain Péanne, Pascale de Lonlay, François Foulquier, et al.
Clinical Chemistry
|
November 25, 2003
N-acetylated metabolites in urine: proton nuclear magnetic resonance spectroscopic study on patients with inborn errors of metabolism
Udo F H Engelke, Maria L F Liebrand-van Sambeek, Jan G N de Jong, et al.
Clinical Chemistry
|
October 28, 2003
Apolipoprotein C-III isofocusing in the diagnosis of genetic defects in O-glycan biosynthesis
Suzan Wopereis, Stephanie Grünewald, Eva Morava, et al.
Molecular Genetics and Metabolism
|
November 10, 2016
Autism in patients with propionic acidemia
Peter Witters, Eric Debbold, Kea Crivelly, et al.
Molecular Genetics and Metabolism
|
June 25, 2024
Cardiomyopathy, an uncommon phenotype of congenital disorders of glycosylation: Recommendations for baseline screening and follow-up evaluation
Roni Zemet, Kyle D Hope, Andrew C Edmondson, et al.
European Journal of Human Genetics : EJHG
|
October 8, 2009
Functional consequences of mitochondrial tRNA Trp and tRNA Arg mutations causing combined OXPHOS defects
Paulien Smits, Sandy Mattijssen, Eva Morava, et al.
Journal of Inherited Metabolic Disease
|
October 19, 2014
TMEM70 deficiency: long-term outcome of 48 patients
Martin Magner, Veronika Dvorakova, Marketa Tesarova, et al.
Molecular Genetics and Metabolism
|
May 24, 2023
Coagulation abnormalities in a prospective cohort of 50 patients with PMM2-congenital disorder of glycosylation
Diederik De Graef, Anna N Ligezka, Joseph Rezents, et al.
Page
of 36