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Experimental Physiology
|
January 21, 2014
Maintaining skeletal muscle mass: lessons learned from hibernation
Evgueni A Ivakine, Ronald D Cohn
NPJ Genomic Medicine
|
May 6, 2026
Bridging the gap: an emerging link between tubulinopathies and ciliopathies
Sydney Steiman, Safia Omer, Stephen Pastore, et al.
Nature Biotechnology
|
January 29, 2024
An optimized toolkit for prime editing
Ryan M Marks, Ori Scott, Evgueni A Ivakine, et al.
Human Gene Therapy
|
April 29, 2023
Advances in CRISPR/Cas9 Genome Editing for the Treatment of Muscular Dystrophies
Sina Fatehi, Ryan M Marks, Matthew J Rok, et al.
NPJ Genomic Medicine
|
May 15, 2021
STAT1 gain-of-function heterozygous cell models reveal diverse interferon-signature gene transcriptional responses
Ori Scott, Kyle Lindsay, Steven Erwood, et al.
Molecular Therapy. Nucleic Acids
|
January 6, 2025
Precise template-free correction restores gene function in Tay-Sachs disease while reframing is ineffective
Joshua E Hung, Reid A Brewer, Lujaina Elbakr, et al.
Genome Research
|
November 23, 2019
Modeling Niemann-Pick disease type C in a human haploid cell line allows for patient variant characterization and clinical interpretation
Steven Erwood, Reid A Brewer, Teija M I Bily, et al.
Diabetes
|
November 30, 2006
The idd4 locus displays sex-specific epistatic effects on type 1 diabetes susceptibility in nonobese diabetic mice
Evgueni A Ivakine, Steven M Mortin-Toth, Omid M Gulban, et al.
Molecular Therapy. Nucleic Acids
|
November 7, 2024
Multi-gene duplication removal in an engineered human cellular MECP2 duplication syndrome model with an <i>IRAK1-MECP2</i> duplication
Samar Z Rizvi, Wing Suen Chan, Eleonora Maino, et al.
Molecular Therapy. Methods & Clinical Development
|
June 4, 2020
Allele-Specific Prevention of Nonsense-Mediated Decay in Cystic Fibrosis Using Homology-Independent Genome Editing
Steven Erwood, Onofrio Laselva, Teija M I Bily, et al.
Page
of 4
Search research articles
Search
Showing results (1-10 of 35) with videos related to
Sort By:
Page
of 4
Experimental Physiology
|
January 21, 2014
Maintaining skeletal muscle mass: lessons learned from hibernation
Evgueni A Ivakine, Ronald D Cohn
NPJ Genomic Medicine
|
May 6, 2026
Bridging the gap: an emerging link between tubulinopathies and ciliopathies
Sydney Steiman, Safia Omer, Stephen Pastore, et al.
Nature Biotechnology
|
January 29, 2024
An optimized toolkit for prime editing
Ryan M Marks, Ori Scott, Evgueni A Ivakine, et al.
Human Gene Therapy
|
April 29, 2023
Advances in CRISPR/Cas9 Genome Editing for the Treatment of Muscular Dystrophies
Sina Fatehi, Ryan M Marks, Matthew J Rok, et al.
NPJ Genomic Medicine
|
May 15, 2021
STAT1 gain-of-function heterozygous cell models reveal diverse interferon-signature gene transcriptional responses
Ori Scott, Kyle Lindsay, Steven Erwood, et al.
Molecular Therapy. Nucleic Acids
|
January 6, 2025
Precise template-free correction restores gene function in Tay-Sachs disease while reframing is ineffective
Joshua E Hung, Reid A Brewer, Lujaina Elbakr, et al.
Genome Research
|
November 23, 2019
Modeling Niemann-Pick disease type C in a human haploid cell line allows for patient variant characterization and clinical interpretation
Steven Erwood, Reid A Brewer, Teija M I Bily, et al.
Diabetes
|
November 30, 2006
The idd4 locus displays sex-specific epistatic effects on type 1 diabetes susceptibility in nonobese diabetic mice
Evgueni A Ivakine, Steven M Mortin-Toth, Omid M Gulban, et al.
Molecular Therapy. Nucleic Acids
|
November 7, 2024
Multi-gene duplication removal in an engineered human cellular MECP2 duplication syndrome model with an <i>IRAK1-MECP2</i> duplication
Samar Z Rizvi, Wing Suen Chan, Eleonora Maino, et al.
Molecular Therapy. Methods & Clinical Development
|
June 4, 2020
Allele-Specific Prevention of Nonsense-Mediated Decay in Cystic Fibrosis Using Homology-Independent Genome Editing
Steven Erwood, Onofrio Laselva, Teija M I Bily, et al.
Page
of 4