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Cell Reports. Medicine
|
January 27, 2023
Severe hematopoietic stem cell inflammation compromises chronic granulomatous disease gene therapy
Steicy Sobrino, Alessandra Magnani, Michaela Semeraro, et al.
Blood
|
December 2, 2010
Clinical similarities and differences of patients with X-linked lymphoproliferative syndrome type 1 (XLP-1/SAP deficiency) versus type 2 (XLP-2/XIAP deficiency)
Jana Pachlopnik Schmid, Danielle Canioni, Despina Moshous, et al.
JAMA
|
April 22, 2015
Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome
Salima Hacein-Bey Abina, H Bobby Gaspar, Johanna Blondeau, et al.
Nature Medicine
|
January 25, 2022
Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: the HGB-205 trial
Elisa Magrin, Michaela Semeraro, Nicolas Hebert, et al.
Human Mutation
|
May 4, 2019
Functional classification of ATM variants in ataxia-telangiectasia patients
Alice Fiévet, Dorine Bellanger, Guillaume Rieunier, et al.
Journal of Clinical Immunology
|
July 9, 2020
Neuroinflammatory Disease as an Isolated Manifestation of Hemophagocytic Lymphohistiocytosis
Annaliesse Blincoe, Maximilian Heeg, Patrick K Campbell, et al.
The Journal of Allergy and Clinical Immunology
|
January 30, 2024
Allogeneic hematopoietic cell transplantation is effective for p47phox chronic granulomatous disease: A Primary Immune Deficiency Treatment Consortium study
Eyal Grunebaum, Danielle E Arnold, Brent Logan, et al.
Transplantation and Cellular Therapy
|
October 4, 2025
Umbilical Cord Blood Transplantation Provides an Alternative for Patients With Chronic Granulomatous Disease Lacking HLA-Matched Donors: A PIDTC Report
Danielle E Arnold, Jennifer W Leiding, Brent Logan, et al.
The New England Journal of Medicine
|
October 9, 2014
A modified γ-retrovirus vector for X-linked severe combined immunodeficiency
Salima Hacein-Bey-Abina, Sung-Yun Pai, H Bobby Gaspar, et al.
The Journal of Allergy and Clinical Immunology
|
November 7, 2023
JAK inhibitor treatment for inborn errors of JAK/STAT signaling: An ESID/EBMT-IEWP retrospective study
Marco Fischer, Peter Olbrich, Jérôme Hadjadj, et al.
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of 6
Search research articles
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Showing results (41-50 of 53) with videos related to
Sort By:
Page
of 6
Cell Reports. Medicine
|
January 27, 2023
Severe hematopoietic stem cell inflammation compromises chronic granulomatous disease gene therapy
Steicy Sobrino, Alessandra Magnani, Michaela Semeraro, et al.
Blood
|
December 2, 2010
Clinical similarities and differences of patients with X-linked lymphoproliferative syndrome type 1 (XLP-1/SAP deficiency) versus type 2 (XLP-2/XIAP deficiency)
Jana Pachlopnik Schmid, Danielle Canioni, Despina Moshous, et al.
JAMA
|
April 22, 2015
Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome
Salima Hacein-Bey Abina, H Bobby Gaspar, Johanna Blondeau, et al.
Nature Medicine
|
January 25, 2022
Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: the HGB-205 trial
Elisa Magrin, Michaela Semeraro, Nicolas Hebert, et al.
Human Mutation
|
May 4, 2019
Functional classification of ATM variants in ataxia-telangiectasia patients
Alice Fiévet, Dorine Bellanger, Guillaume Rieunier, et al.
Journal of Clinical Immunology
|
July 9, 2020
Neuroinflammatory Disease as an Isolated Manifestation of Hemophagocytic Lymphohistiocytosis
Annaliesse Blincoe, Maximilian Heeg, Patrick K Campbell, et al.
The Journal of Allergy and Clinical Immunology
|
January 30, 2024
Allogeneic hematopoietic cell transplantation is effective for p47phox chronic granulomatous disease: A Primary Immune Deficiency Treatment Consortium study
Eyal Grunebaum, Danielle E Arnold, Brent Logan, et al.
Transplantation and Cellular Therapy
|
October 4, 2025
Umbilical Cord Blood Transplantation Provides an Alternative for Patients With Chronic Granulomatous Disease Lacking HLA-Matched Donors: A PIDTC Report
Danielle E Arnold, Jennifer W Leiding, Brent Logan, et al.
The New England Journal of Medicine
|
October 9, 2014
A modified γ-retrovirus vector for X-linked severe combined immunodeficiency
Salima Hacein-Bey-Abina, Sung-Yun Pai, H Bobby Gaspar, et al.
The Journal of Allergy and Clinical Immunology
|
November 7, 2023
JAK inhibitor treatment for inborn errors of JAK/STAT signaling: An ESID/EBMT-IEWP retrospective study
Marco Fischer, Peter Olbrich, Jérôme Hadjadj, et al.
Page
of 6