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Frontiers in Immunology|June 20, 2019
Corrigendum: Targeted NGS Platforms for Genetic Screening and Gene Discovery in Primary ImmunodeficienciesCristina Cifaldi, Immacolata Brigida, Federica Barzaghi, et al.The Lancet. Haematology|April 15, 2019
Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical studyFrancesca Ferrua, Maria Pia Cicalese, Stefania Galimberti, et al.Nature Communications|April 30, 2024
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCIDDaniela Cesana, Maria Pia Cicalese, Andrea Calabria, et al.Science Translational Medicine|May 1, 2024
Early skeletal outcomes after hematopoietic stem and progenitor cell gene therapy for Hurler syndromeGiulia Consiglieri, Francesca Tucci, Maurizio De Pellegrin, et al.Lancet (London, England)|January 23, 2022
Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded accessFrancesca Fumagalli, Valeria Calbi, Maria Grazia Natali Sora, et al.Blood|September 27, 2018
T-cell defects in patients with ARPC1B germline mutations account for combined immunodeficiencyImmacolata Brigida, Matteo Zoccolillo, Maria Pia Cicalese, et al.The New England Journal of Medicine|November 17, 2021
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler SyndromeBernhard Gentner, Francesca Tucci, Stefania Galimberti, et al.The New England Journal of Medicine|April 23, 2025
Long-Term Effects of Atidarsagene Autotemcel for Metachromatic LeukodystrophyFrancesca Fumagalli, Valeria Calbi, Vera Gallo, et al.Journal of Clinical Immunology|July 29, 2021
Hematopoietic Cell Transplantation Cures Adenosine Deaminase 2 Deficiency: Report on 30 PatientsHasan Hashem, Giorgia Bucciol, Seza Ozen, et al.European Journal of Immunology|May 14, 2022
Follicular helper T cell signature of replicative exhaustion, apoptosis, and senescence in common variable immunodeficiencyGiulia Milardi, Biagio Di Lorenzo, Jolanda Gerosa, et al.Pageof 8