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Federico Mingozzi

Showing results (21-30 of 138) with videos related to

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Journal of Clinical Medicine|July 2, 2021
Emerging Immunogenicity and Genotoxicity Considerations of Adeno-Associated Virus Vector Gene Therapy for HemophiliaPaul E Monahan, Claude Négrier, Michael Tarantino, et al.
Human Gene Therapy Methods|March 31, 2015
Determination of anti-adeno-associated virus vector neutralizing antibody titer with an in vitro reporter systemAmine Meliani, Christian Leborgne, Sabrina Triffault, et al.
Proceedings of the National Academy of Sciences of the United States of America|March 16, 2006
Prevention of cytotoxic T lymphocyte responses to factor IX-expressing hepatocytes by gene transfer-induced regulatory T cellsEric Dobrzynski, Julie C Fitzgerald, Ou Cao, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|October 6, 2025
Overcoming barriers to commercially pre-viable gene and cell therapies for rare and ultra-rare diseasesDavid Barrett, Paula M Cannon, Federico Mingozzi, et al.
Human Gene Therapy|March 23, 2019
Alpha-1-Antitrypsin Promoter Improves the Efficacy of an Adeno-Associated Virus Vector for the Treatment of Mitochondrial Neurogastrointestinal EncephalomyopathyRaquel Cabrera-Pérez, Ferran Vila-Julià, Michio Hirano, et al.
Molecular Therapy. Methods & Clinical Development|March 28, 2017
Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance InductionSang-Oh Han, Giuseppe Ronzitti, Benjamin Arnson, et al.
Molecular Therapy. Methods & Clinical Development|May 11, 2019
Erratum: Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance InductionSang-Oh Han, Giuseppe Ronzitti, Benjamin Arnson, et al.
JIMD Reports|February 19, 2015
Innate and Adaptive Immune Response in Fabry DiseaseWladimir Mauhin, Olivier Lidove, Elisa Masat, et al.
Thrombosis and Haemostasis|June 5, 2003
A FV multiallelic marker detects genetic components of APC resistance contributing to venous thromboembolism in FV Leiden carriersFederico Mingozzi, Cristina Legnani, Barbara Lunghi, et al.
Human Gene Therapy|June 28, 2007
Muscle as a target for supplementary factor IX gene transferBrad E Hoffman, Eric Dobrzynski, Lixin Wang, et al.
Pageof 14

Showing results (21-30 of 138) with videos related to

Sort By:
Pageof 14
Journal of Clinical Medicine|July 2, 2021
Emerging Immunogenicity and Genotoxicity Considerations of Adeno-Associated Virus Vector Gene Therapy for HemophiliaPaul E Monahan, Claude Négrier, Michael Tarantino, et al.
Human Gene Therapy Methods|March 31, 2015
Determination of anti-adeno-associated virus vector neutralizing antibody titer with an in vitro reporter systemAmine Meliani, Christian Leborgne, Sabrina Triffault, et al.
Proceedings of the National Academy of Sciences of the United States of America|March 16, 2006
Prevention of cytotoxic T lymphocyte responses to factor IX-expressing hepatocytes by gene transfer-induced regulatory T cellsEric Dobrzynski, Julie C Fitzgerald, Ou Cao, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|October 6, 2025
Overcoming barriers to commercially pre-viable gene and cell therapies for rare and ultra-rare diseasesDavid Barrett, Paula M Cannon, Federico Mingozzi, et al.
Human Gene Therapy|March 23, 2019
Alpha-1-Antitrypsin Promoter Improves the Efficacy of an Adeno-Associated Virus Vector for the Treatment of Mitochondrial Neurogastrointestinal EncephalomyopathyRaquel Cabrera-Pérez, Ferran Vila-Julià, Michio Hirano, et al.
Molecular Therapy. Methods & Clinical Development|March 28, 2017
Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance InductionSang-Oh Han, Giuseppe Ronzitti, Benjamin Arnson, et al.
Molecular Therapy. Methods & Clinical Development|May 11, 2019
Erratum: Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance InductionSang-Oh Han, Giuseppe Ronzitti, Benjamin Arnson, et al.
JIMD Reports|February 19, 2015
Innate and Adaptive Immune Response in Fabry DiseaseWladimir Mauhin, Olivier Lidove, Elisa Masat, et al.
Thrombosis and Haemostasis|June 5, 2003
A FV multiallelic marker detects genetic components of APC resistance contributing to venous thromboembolism in FV Leiden carriersFederico Mingozzi, Cristina Legnani, Barbara Lunghi, et al.
Human Gene Therapy|June 28, 2007
Muscle as a target for supplementary factor IX gene transferBrad E Hoffman, Eric Dobrzynski, Lixin Wang, et al.
Pageof 14