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Developmental Medicine and Child Neurology
|
June 16, 2018
Duchenne muscular dystrophy and caregiver burden: a systematic review
Erik Landfeldt, Josefin Edström, Filippo Buccella, et al.
Annali Dell'Istituto Superiore Di Sanita
|
June 16, 2017
A harmonized and efficient clinical research environment would benefit patients and enhance European competitiveness. Commentary
Antonino Amato, Eugenio Aringhieri, Stefania Boccia, et al.
Journal of Comparative Effectiveness Research
|
August 16, 2019
Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy: patient demographics and characteristics from the STRIDE Registry
Francesco Muntoni, Isabelle Desguerre, Michela Guglieri, et al.
Journal of Comparative Effectiveness Research
|
January 31, 2020
Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study
Eugenio Mercuri, Francesco Muntoni, Andrés Nascimento Osorio, et al.
Journal of Neurology
|
April 28, 2023
Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015-2022): 2022 interim analysis
Eugenio Mercuri, Andrés Nascimento Osorio, Francesco Muntoni, et al.
Journal of Neuromuscular Diseases
|
February 20, 2025
A Parent Project Muscular Dystrophy-sponsored International Workshop Report on Endocrine and Bone Issues in Patients with Duchenne Muscular Dystrophy: An Ever-changing Landscape
Leanne M Ward, David R Weber, Sze Choong Wong, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
February 1, 2025
Transition of patients with Duchenne muscular dystrophy from paediatric to adult care: An international Delphi consensus study
Diana Castro, Thomas Sejersen, Luca Bello, et al.
Human Mutation
|
January 22, 2015
The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations
Catherine L Bladen, David Salgado, Soledad Monges, et al.
Journal of Neuromuscular Diseases
|
November 11, 2017
Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database
Zaïda Koeks, Catherine L Bladen, David Salgado, et al.
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of 1
Search research articles
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Showing results (1-10 of 9) with videos related to
Sort By:
Page
of 1
Developmental Medicine and Child Neurology
|
June 16, 2018
Duchenne muscular dystrophy and caregiver burden: a systematic review
Erik Landfeldt, Josefin Edström, Filippo Buccella, et al.
Annali Dell'Istituto Superiore Di Sanita
|
June 16, 2017
A harmonized and efficient clinical research environment would benefit patients and enhance European competitiveness. Commentary
Antonino Amato, Eugenio Aringhieri, Stefania Boccia, et al.
Journal of Comparative Effectiveness Research
|
August 16, 2019
Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy: patient demographics and characteristics from the STRIDE Registry
Francesco Muntoni, Isabelle Desguerre, Michela Guglieri, et al.
Journal of Comparative Effectiveness Research
|
January 31, 2020
Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study
Eugenio Mercuri, Francesco Muntoni, Andrés Nascimento Osorio, et al.
Journal of Neurology
|
April 28, 2023
Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015-2022): 2022 interim analysis
Eugenio Mercuri, Andrés Nascimento Osorio, Francesco Muntoni, et al.
Journal of Neuromuscular Diseases
|
February 20, 2025
A Parent Project Muscular Dystrophy-sponsored International Workshop Report on Endocrine and Bone Issues in Patients with Duchenne Muscular Dystrophy: An Ever-changing Landscape
Leanne M Ward, David R Weber, Sze Choong Wong, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|
February 1, 2025
Transition of patients with Duchenne muscular dystrophy from paediatric to adult care: An international Delphi consensus study
Diana Castro, Thomas Sejersen, Luca Bello, et al.
Human Mutation
|
January 22, 2015
The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations
Catherine L Bladen, David Salgado, Soledad Monges, et al.
Journal of Neuromuscular Diseases
|
November 11, 2017
Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database
Zaïda Koeks, Catherine L Bladen, David Salgado, et al.
Page
of 1