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Clinical Infectious Diseases : an Official Publication of the Infectious Diseases Society of America|May 3, 2018
Genomic Surveillance Reveals Diversity of Multidrug-Resistant Organism Colonization and Infection: A Prospective Cohort Study in Liver Transplant RecipientsNenad Macesic, Angela Gomez-Simmonds, Sean B Sullivan, et al.The New England Journal of Medicine|November 2, 2017
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular AtrophyRichard S Finkel, Eugenio Mercuri, Basil T Darras, et al.Plos One|March 20, 2018
Skeletal muscle magnetic resonance biomarkers correlate with function and sentinel events in Duchenne muscular dystrophyAlison M Barnard, Rebecca J Willcocks, Erika L Finanger, et al.Muscle & Nerve|April 27, 2019
Balance impairment in pediatric charcot-marie-tooth diseaseTimothy Estilow, Allan M Glanzman, Joshua Burns, et al.Nature|August 1, 2014
DNA-damage-induced differentiation of leukaemic cells as an anti-cancer barrierMargarida A Santos, Robert B Faryabi, Aysegul V Ergen, et al.Biorxiv : the Preprint Server for Biology|July 9, 2025
An Intrinsic-hoc Framework for Heterogeneous Cellular Senescence Elucidation Using Deep Graph Representation Learning and Experimental ValidationAnjun Ma, Hao Cheng, Natalia Del Pilar Vanegas, et al.Neuromuscular Disorders : NMD|January 2, 2018
Diagnosis and management of spinal muscular atrophy: Part 1: Recommendations for diagnosis, rehabilitation, orthopedic and nutritional careEugenio Mercuri, Richard S Finkel, Francesco Muntoni, et al.The New England Journal of Medicine|August 13, 2025
Risdiplam in Presymptomatic Spinal Muscular AtrophyRichard S Finkel, Laurent Servais, Dmitry Vlodavets, et al.Circulation|June 14, 2024
Endothelial Heterogeneity in the Response to Autophagy Drives Small Vessel Muscularization in Pulmonary HypertensionQi Zhang, Nobuhiro Yaoita, Arata Tabuchi, et al.JCI Insight|February 10, 2025
Regulation of lung progenitor plasticity and repair by fatty acid oxidationQuetzalli D Angeles-Lopez, Jhonny Rodriguez-Lopez, Paula Agudelo Garcia, et al.Pageof 202