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The Journal of Pediatrics|September 21, 2021
Evidence of Treatment Benefits in Patients with Mucopolysaccharidosis Type I-Hurler in Long-term Follow-up Using a New Magnetic Resonance Imaging Scoring SystemSilvia Pontesilli, Cristina Baldoli, Pasquale Anthony Della Rosa, et al.
British Journal of Haematology|April 21, 2015
Long-term results of high-dose imatinib in children and adolescents with chronic myeloid leukaemia in chronic phase: the Italian experienceFiorina Giona, Maria C Putti, Concetta Micalizzi, et al.
The Journal of Allergy and Clinical Immunology|December 25, 2019
Treatment with rapamycin can restore regulatory T-cell function in IPEX patientsLaura Passerini, Federica Barzaghi, Rosalia Curto, et al.
Molecular Therapy. Methods & Clinical Development|September 6, 2021
Peripheral blood stem and progenitor cell collection in pediatric candidates for ex vivo gene therapy: a 10-year seriesDaniele Canarutto, Francesca Tucci, Salvatore Gattillo, et al.
Biomedicines|July 29, 2023
Outcome of BCG Vaccination in ADA-SCID Patients: A 12-Patient SeriesDaniele Canarutto, Chiara Oltolini, Federica Barzaghi, et al.
Frontiers in Pharmacology|August 8, 2026
Busulfan exposure variability and acute toxicity in pediatric patients undergoing hematopoietic stem cell gene therapyDaniele Canarutto, Simona De Gregori, Salvatore Recupero, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|May 27, 2026
Ex Vivo Expansion of Hematopoietic Stem and Progenitor Cells from Human Mobilized Peripheral Blood for Gene Therapy ApplicationsErika Zonari, Matteo Maria Naldini, Matteo Barcella, et al.
BMC Gastroenterology|February 13, 2014
Celiac disease in the Mediterranean areaFrancesca Tucci, Luca Astarita, Abdelhak Abkari, et al.
Haematologica|August 21, 2020
Emapalumab treatment in an ADA-SCID patient with refractory hemophagocytic lymphohistiocytosis-related graft failure and disseminated bacillus Calmette-Guérin infectionFrancesca Tucci, Vera Gallo, Federica Barzaghi, et al.
Journal of Clinical Immunology|August 9, 2022
A Novel Assay in Whole Blood Demonstrates Restoration of Mitochondrial Activity in Phagocytes After Successful HSCT in Hyperinflamed X-Linked Chronic Granulomatous DiseaseMaddalena Migliavacca, Luca Basso Ricci, Giada Farinelli, et al.
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