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International Journal of Molecular Sciences
|
February 25, 2023
Long-Term <i>SMN</i>- and <i>Ncald</i>-ASO Combinatorial Therapy in SMA Mice and <i>NCALD</i>-ASO Treatment in hiPSC-Derived Motor Neurons Show Protective Effects
Anixa Muiños-Bühl, Roman Rombo, Karen K Ling, et al.
Neurobiology of Disease
|
December 15, 2019
Knockdown of GADD34 in neonatal mutant SOD1 mice ameliorates ALS
Ghanashyam D Ghadge, Yoshifumi Sonobe, Adrian Camarena, et al.
Molecular Therapy. Nucleic Acids
|
July 24, 2025
Antisense oligonucleotide therapy for patients with Friedreich's ataxia carrying the c.165+5G>C splicing mutation
Pouiré Yameogo, Selina Aguilar, Thazha P Prakash, et al.
Genes & Development
|
July 14, 2010
Antisense correction of SMN2 splicing in the CNS rescues necrosis in a type III SMA mouse model
Yimin Hua, Kentaro Sahashi, Gene Hung, et al.
Bioorganic & Medicinal Chemistry Letters
|
August 5, 2018
Activating frataxin expression by single-stranded siRNAs targeting the GAA repeat expansion
Xiulong Shen, Audrius Kilikevicius, Daniel O'Reilly, et al.
Nucleic Acids Research
|
December 6, 2019
Hybridization-mediated off-target effects of splice-switching antisense oligonucleotides
Juergen Scharner, Wai Kit Ma, Qian Zhang, et al.
Nucleic Acids Research
|
April 20, 2018
Antisense oligonucleotides correct the familial dysautonomia splicing defect in IKBKAP transgenic mice
Rahul Sinha, Young Jin Kim, Tomoki Nomakuchi, et al.
RNA (New York, N.Y.)
|
June 2, 2019
Efficient electroporation of neuronal cells using synthetic oligonucleotides: identifying duplex RNA and antisense oligonucleotide activators of human frataxin expression
Xiulong Shen, Sharon Beasley, Jennifer N Putman, et al.
Journal of the Association for Research in Otolaryngology : JARO
|
October 14, 2017
Rescue of Outer Hair Cells with Antisense Oligonucleotides in Usher Mice Is Dependent on Age of Treatment
Abhilash Ponnath, Frederic F Depreux, Francine M Jodelka, et al.
Biochemistry
|
December 15, 2004
Stereochemistry of glutamate receptor agonist efficacy: engineering a dual-specificity AMPA/kainate receptor
Dean R Madden, Qing Cheng, Shalita Thiran, et al.
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Search research articles
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Showing results (31-40 of 163) with videos related to
Sort By:
Page
of 17
International Journal of Molecular Sciences
|
February 25, 2023
Long-Term <i>SMN</i>- and <i>Ncald</i>-ASO Combinatorial Therapy in SMA Mice and <i>NCALD</i>-ASO Treatment in hiPSC-Derived Motor Neurons Show Protective Effects
Anixa Muiños-Bühl, Roman Rombo, Karen K Ling, et al.
Neurobiology of Disease
|
December 15, 2019
Knockdown of GADD34 in neonatal mutant SOD1 mice ameliorates ALS
Ghanashyam D Ghadge, Yoshifumi Sonobe, Adrian Camarena, et al.
Molecular Therapy. Nucleic Acids
|
July 24, 2025
Antisense oligonucleotide therapy for patients with Friedreich's ataxia carrying the c.165+5G>C splicing mutation
Pouiré Yameogo, Selina Aguilar, Thazha P Prakash, et al.
Genes & Development
|
July 14, 2010
Antisense correction of SMN2 splicing in the CNS rescues necrosis in a type III SMA mouse model
Yimin Hua, Kentaro Sahashi, Gene Hung, et al.
Bioorganic & Medicinal Chemistry Letters
|
August 5, 2018
Activating frataxin expression by single-stranded siRNAs targeting the GAA repeat expansion
Xiulong Shen, Audrius Kilikevicius, Daniel O'Reilly, et al.
Nucleic Acids Research
|
December 6, 2019
Hybridization-mediated off-target effects of splice-switching antisense oligonucleotides
Juergen Scharner, Wai Kit Ma, Qian Zhang, et al.
Nucleic Acids Research
|
April 20, 2018
Antisense oligonucleotides correct the familial dysautonomia splicing defect in IKBKAP transgenic mice
Rahul Sinha, Young Jin Kim, Tomoki Nomakuchi, et al.
RNA (New York, N.Y.)
|
June 2, 2019
Efficient electroporation of neuronal cells using synthetic oligonucleotides: identifying duplex RNA and antisense oligonucleotide activators of human frataxin expression
Xiulong Shen, Sharon Beasley, Jennifer N Putman, et al.
Journal of the Association for Research in Otolaryngology : JARO
|
October 14, 2017
Rescue of Outer Hair Cells with Antisense Oligonucleotides in Usher Mice Is Dependent on Age of Treatment
Abhilash Ponnath, Frederic F Depreux, Francine M Jodelka, et al.
Biochemistry
|
December 15, 2004
Stereochemistry of glutamate receptor agonist efficacy: engineering a dual-specificity AMPA/kainate receptor
Dean R Madden, Qing Cheng, Shalita Thiran, et al.
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of 17