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Fulvio Mavilio

Showing results (51-60 of 87) with videos related to

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Translational Research : the Journal of Laboratory and Clinical Medicine|July 30, 2017
Evaluation of tolerance to lentiviral LV-RPE65 gene therapy vector after subretinal delivery in non-human primatesAlexandre Matet, Corinne Kostic, Alexis-Pierre Bemelmans, et al.
American Journal of Human Genetics|September 6, 2023
High-throughput transcriptome analyses from ASPIRO, a phase 1/2/3 study of gene replacement therapy for X-linked myotubular myopathyGaia Andreoletti, Oriana Romano, Hsin-Jung Chou, et al.
Molecular Therapy. Nucleic Acids|April 24, 2023
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategiesMégane Brusson, Anne Chalumeau, Pierre Martinucci, et al.
Blood Advances|February 26, 2021
Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cellsGiulia Pavani, Anna Fabiano, Marine Laurent, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 14, 2013
Targeted gene addition in human epithelial stem cells by zinc-finger nuclease-mediated homologous recombinationAndrea Coluccio, Francesca Miselli, Angelo Lombardo, et al.
Plos One|May 16, 2015
Genome-Wide Definition of Promoter and Enhancer Usage during Neural Induction of Human Embryonic Stem CellsValentina Poletti, Alessia Delli Carri, Guidantonio Malagoli Tagliazucchi, et al.
Blood|May 18, 2007
Hot spots of retroviral integration in human CD34+ hematopoietic cellsClaudia Cattoglio, Giulia Facchini, Daniela Sartori, et al.
Proceedings of the National Academy of Sciences of the United States of America|January 25, 2006
Retroviral vector integration deregulates gene expression but has no consequence on the biology and function of transplanted T cellsAlessandra Recchia, Chiara Bonini, Zulma Magnani, et al.
Blood|August 5, 2009
Integration of retroviral vectors induces minor changes in the transcriptional activity of T cells from ADA-SCID patients treated with gene therapyBarbara Cassani, Eugenio Montini, Giulietta Maruggi, et al.
Molecular Therapy. Methods & Clinical Development|November 14, 2019
Biosafety Studies of a Clinically Applicable Lentiviral Vector for the Gene Therapy of Artemis-SCIDSabine Charrier, Chantal Lagresle-Peyrou, Valentina Poletti, et al.
Pageof 9

Showing results (51-60 of 87) with videos related to

Sort By:
Pageof 9
Translational Research : the Journal of Laboratory and Clinical Medicine|July 30, 2017
Evaluation of tolerance to lentiviral LV-RPE65 gene therapy vector after subretinal delivery in non-human primatesAlexandre Matet, Corinne Kostic, Alexis-Pierre Bemelmans, et al.
American Journal of Human Genetics|September 6, 2023
High-throughput transcriptome analyses from ASPIRO, a phase 1/2/3 study of gene replacement therapy for X-linked myotubular myopathyGaia Andreoletti, Oriana Romano, Hsin-Jung Chou, et al.
Molecular Therapy. Nucleic Acids|April 24, 2023
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategiesMégane Brusson, Anne Chalumeau, Pierre Martinucci, et al.
Blood Advances|February 26, 2021
Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cellsGiulia Pavani, Anna Fabiano, Marine Laurent, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 14, 2013
Targeted gene addition in human epithelial stem cells by zinc-finger nuclease-mediated homologous recombinationAndrea Coluccio, Francesca Miselli, Angelo Lombardo, et al.
Plos One|May 16, 2015
Genome-Wide Definition of Promoter and Enhancer Usage during Neural Induction of Human Embryonic Stem CellsValentina Poletti, Alessia Delli Carri, Guidantonio Malagoli Tagliazucchi, et al.
Blood|May 18, 2007
Hot spots of retroviral integration in human CD34+ hematopoietic cellsClaudia Cattoglio, Giulia Facchini, Daniela Sartori, et al.
Proceedings of the National Academy of Sciences of the United States of America|January 25, 2006
Retroviral vector integration deregulates gene expression but has no consequence on the biology and function of transplanted T cellsAlessandra Recchia, Chiara Bonini, Zulma Magnani, et al.
Blood|August 5, 2009
Integration of retroviral vectors induces minor changes in the transcriptional activity of T cells from ADA-SCID patients treated with gene therapyBarbara Cassani, Eugenio Montini, Giulietta Maruggi, et al.
Molecular Therapy. Methods & Clinical Development|November 14, 2019
Biosafety Studies of a Clinically Applicable Lentiviral Vector for the Gene Therapy of Artemis-SCIDSabine Charrier, Chantal Lagresle-Peyrou, Valentina Poletti, et al.
Pageof 9