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Blood|June 17, 1998
Adeno-associated viral vector-mediated gene transfer of human blood coagulation factor IX into mouse liverH Nakai, R W Herzog, J N Hagstrom, et al.Nature Medicine|January 12, 1999
Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vectorR W Herzog, E Y Yang, L B Couto, et al.Pageof 3